Determining off-target effects of splice-switching antisense oligonucleotides using short read RNAseq in neuronally differentiated human induced pluripotent stem cells
利用短读长RNA测序技术在神经分化的人类诱导多能干细胞中确定剪接转换反义寡核苷酸的脱靶效应
期刊:Human Molecular Genetics
影响因子:3.2
doi:10.1093/hmg/ddaf153
Kuijper, Elsa C; van der Graaf, Linda; Pepers, Barry A; Guimarães Ramos, Mariana; Korhorn, Sylvia; Toonen, Lodewijk J A; Cats, Davy; Buijsen, Ronald A M; Mina, Eleni; Mei, Hailiang; van Roon-Mom, Willeke M C