Incorporating Patient Perspectives into a Composite Score for Measuring Disease Progression in Spinocerebellar Ataxia (SCA)
将患者视角纳入综合评分以衡量脊髓小脑性共济失调(SCA)的疾病进展
期刊:Neurology and Therapy
影响因子:4.8
doi:10.1007/s40120-026-00891-6
Potashman, Michele H; Rogula, Basia M; Powell, Lauren C; Korol, Ellen E; Dickson, Sam P; Hendrix, Suzanne; Heinrich, Maggie; Rudell, Katja; Abetz-Webb, Linda; Beiner, Melissa W; Coric, Vlad; Rosenthal, Liana S; Perlman, Susan L; Schmahmann, Jeremy D; L'Italien, Gil