Real-world safety and efficacy of rADAMTS13 prophylaxis in congenital thrombotic thrombocytopenic purpura: experience from Polish patients previously treated with fresh frozen plasma
rADAMTS13预防先天性血栓性血小板减少性紫癜的真实世界安全性和有效性:来自既往接受过新鲜冰冻血浆治疗的波兰患者的经验
期刊:Haematologica
影响因子:7.9
doi:10.3324/haematol.2025.288561
Windyga, Jerzy; Zdziarska, Joanna; Górska-Kosicka, Magdalena; Gwozdowska, Adela; Jazdon, Miłosz; Łaguna, Paweł; Szczepańska, Maria; Wojdalska, Magdalena; Pietrys, Danuta; Taszner, Michał; Witkowski, Michał; Baran, Beata; Młynarski, Wojciech