Clinically Important Endpoints in Individuals With Leukodystrophy: A Multisite Study
脑白质营养不良患者的临床重要终点:一项多中心研究
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doi:10.1002/cns3.70025
Kotes, Emma R; Woidill, Sarah; D'Aiello, Russell; Khan, Amina; McCann, Jacob; Ramos, Mark; Gavazzi, Francesco; Keller, Stephanie; Van Haren, Keith; Fatemi, Ali; Eichler, Florian; Bonkowsky, Joshua; Fraser, Jamie; Emrick, Lisa; Sherbini, Omar; Hackett, Ashley; Gauna, Jeilo; Amos, Dandre; Goodman, Jordan; Fine, Amena Smith; Nagy, Amanda; Lee, Seungil; Page, Nicole; Schmidt, Johanna; Pizzino, Amy; Muirhead, Kayla; Bennett, Mariko; Waldman, Amy; Shults, Justine; Adang, Laura; Grundmeier, Robert; Vanderver, Adeline