Laterally spreading AAV.SPR enables safe and efficient RS1 delivery to the macula after peripheral subretinal injection
横向扩散的AAV.SPR可在周边视网膜下注射后安全有效地将RS1递送至黄斑。
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2026.03.014
Andres-Mateos, Eva; Kozlowski, Christopher; Zhang, Hangning; Fajardo, Diego; Xu, Emily; Enamorado, Ignacio Navas; Calabro, Kaitlyn R; Rayaprolu, Sruti; Havlik, L Patrick; Handy, Tess E; Plummer, Caryn E; Stevenson, Victoria; Rind, Howard; Leahy, Matthew; Boyd, Ryan F; Coleman, Kirsten E; Boye, Sanford L; Boye, Shannon E