Base editing rescue of spinal muscular atrophy in cells and in mice
碱基编辑可挽救细胞和小鼠脊髓性肌萎缩症
期刊:Science
影响因子:44.7
doi:10.1126/science.adg6518
Mandana Arbab #,Zaneta Matuszek #,Kaitlyn M Kray,Ailing Du,Gregory A Newby,Anton J Blatnik,Aditya Raguram,Michelle F Richter,Kevin T Zhao,Jonathan M Levy,Max W Shen,W David Arnold,Dan Wang,Jun Xie,Guangping Gao,Arthur H M Burghes,David R Liu