Dose-finding and in vivo safety study of an adipose targeted leptin gene therapy for congenital leptin deficiency.
针对先天性瘦素缺乏症的脂肪组织靶向瘦素基因疗法的剂量探索和体内安全性研究
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2025.101500
Huang Wei, Mohammed Tawfiq, Zou Xunchang, Krishnan Anya A, Mo Xiaokui, Xiao Min, Cao Lei