Pervasive supply of therapeutic lysosomal enzymes in the CNS of normal and Krabbe-affected non-human primates by intracerebral lentiviral gene therapy
通过脑内慢病毒基因疗法,在正常和患有克拉伯病的非人灵长类动物的中枢神经系统中广泛供应治疗性溶酶体酶。
期刊:EMBO Molecular Medicine
影响因子:9
doi:10.15252/emmm.201505850
Vasco Meneghini ,Annalisa Lattanzi ,Luigi Tiradani ,Gabriele Bravo ,Francesco Morena ,Francesca Sanvito ,Andrea Calabria ,John Bringas ,Jeanne M Fisher-Perkins ,Jason P Dufour ,Kate C Baker ,Claudio Doglioni ,Eugenio Montini ,Bruce A Bunnell ,Krystof Bankiewicz ,Sabata Martino ,Luigi Naldini ,Angela Gritti