日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Endocrinological complications of Duchenne muscular dystrophy and their subjective burden: observational study evaluating growth, puberty, and bone health

杜氏肌营养不良症的内分泌并发症及其主观负担:一项评估生长、青春期和骨骼健康的观察性研究

Rohlenova, Marie; Haberlova, Jana; Holotova, Petra; Kumhera, Marketa; Simkova, Lucie; Lauerova, Barbora; Svabova, Iveta; Soucek, Ondrej

Patients' Perceptions of Nusinersen Effects According to Their Responder Status

根据患者对诺西那生(Nusinersen)的反应状态,患者对诺西那生疗效的感知

Lilien, Charlotte; Vrscaj, Eva; Thapaliya, Gita; Deconinck, Nicolas; De Waele, Liesbeth; Duong, Tina; Haberlová, Jana; Kumhera, Markéta; Peirens, Geertrui; Szabo, Lena; Tahon, Valentine; Tang, Whitney J; Benmhammed, Noor; Médard, Laurie; Servais, Laurent