Efficacy and Safety of Aficamten in Children and Adolescents With Obstructive Hypertrophic Cardiomyopathy: Study Design and Rationale of CEDAR-HCM
Aficamten治疗儿童和青少年梗阻性肥厚型心肌病的疗效和安全性:CEDAR-HCM研究的设计和原理
期刊:Circulation-Heart Failure
影响因子:8.4
doi:10.1161/CIRCHEARTFAILURE.125.013418
Kaski, Juan Pablo; Kantor, Paul F; Nakano, Stephanie J; Olivotto, Iacopo; Russell, Mark W; Godown, Justin; Chiu, Michael; German, Polina; Heitner, Stephen B; Jacoby, Daniel L; Kupfer, Stuart; Lutz, Justin; Maharao, Neha; Malik, Fady I; Melloni, Chiara; Nieto Morales, Paula F; Simkins, Tyrell; Wei, Jenny; Ho, Carolyn Y