日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Efficacy and Safety of Aficamten in Children and Adolescents With Obstructive Hypertrophic Cardiomyopathy: Study Design and Rationale of CEDAR-HCM

Aficamten治疗儿童和青少年梗阻性肥厚型心肌病的疗效和安全性:CEDAR-HCM研究的设计和原理

Kaski, Juan Pablo; Kantor, Paul F; Nakano, Stephanie J; Olivotto, Iacopo; Russell, Mark W; Godown, Justin; Chiu, Michael; German, Polina; Heitner, Stephen B; Jacoby, Daniel L; Kupfer, Stuart; Lutz, Justin; Maharao, Neha; Malik, Fady I; Melloni, Chiara; Nieto Morales, Paula F; Simkins, Tyrell; Wei, Jenny; Ho, Carolyn Y

Clinical Evaluation of Drug-Drug Interactions With Aficamten

阿菲卡门药物相互作用的临床评价

Maharao, Neha; Xu, Donghong; Divanji, Punag; Simkins, Tyrell J; Li, Jianlin; Dumitrescu, Camelia; Solanki, Priyanka; Griffith, Adrienne; Heitner, Stephen B; Kupfer, Stuart; German, Polina; Lutz, Justin D

Efficacy of aficamten in patients with obstructive hypertrophic cardiomyopathy and mild symptoms: results from the SEQUOIA-HCM trial

阿菲卡坦治疗梗阻性肥厚型心肌病伴轻度症状患者的疗效:SEQUOIA-HCM试验结果

Maron, Martin S; Gimeno, Juan Ramon; Veselka, Josef; Barriales-Villa, Roberto; Claggett, Brian L; Coats, Caroline J; Hegde, Sheila M; Januzzi, James L; Kulac, Ian J; Masri, Ahmad; Nassif, Michael E; Spertus, John A; Jacoby, Daniel L; Heitner, Stephen B; Kupfer, Stuart; Malik, Fady I; Wohltman, Amy; Olivotto, Iacopo

Reldesemtiv in Amyotrophic Lateral Sclerosis: Results From the COURAGE-ALS Randomized Clinical Trial

Reldesemtiv治疗肌萎缩侧索硬化症:COURAGE-ALS随机临床试验结果

Shefner, Jeremy M; Cudkowicz, Merit E; Genge, Angela; Hardiman, Orla; Al-Chalabi, Ammar; Andrews, Jinsy A; Chio, Adriano; Corcia, Philippe; Couratier, Philippe; de Carvalho, Mamede; Heiman-Patterson, Terry; Henderson, Robert D; Ingre, Caroline; Johnston, Wendy; Ludolph, Albert; Maragakis, Nicholas J; Miller, Timothy M; Mora, Jesus S; Petri, Susanne; Simmons, Zachary; van den Berg, Leonard H; Zinman, Lorne; Kupfer, Stuart; Malik, Fady I; Meng, Lisa; Simkins, Tyrell J; Wei, Jenny; Wolff, Andrew A; Rudnicki, Stacy A

Correction: Effect of Hepatic Impairment or Renal Impairment on the Pharmacokinetics of Aficamten

更正:肝功能损害或肾功能损害对阿菲卡门药代动力学的影响

Xu, Donghong; Lutz, Justin D; Divanji, Punag; Li, Jianlin; Benattia, Youcef; Griffith, Adrienne; Heitner, Stephen B; Kupfer, Stuart; German, Polina

Effect of Hepatic Impairment or Renal Impairment on the Pharmacokinetics of Aficamten

肝功能损害或肾功能损害对阿菲卡门药代动力学的影响

Xu, Donghong; Lutz, Justin D; Divanji, Punag; Li, Jianlin; Benattia, Youcef; Griffith, Adrienne; Heitner, Stephen B; Kupfer, Stuart; German, Polina

Toward a Quantitative Understanding of Aficamten Clinical Pharmacology: Population Pharmacokinetic Modeling

迈向对阿菲卡门临床药理学的定量理解:群体药代动力学建模

Xu, Donghong; Li, Hanbin; Heitner, Stephen B; Jacoby, Daniel L; Kupfer, Stuart; German, Polina; Lutz, Justin

Clinical Evaluation of the Effect of Aficamten on QT/QTc Interval in Healthy Participants

阿菲卡坦对健康受试者QT/QTc间期影响的临床评价

Maharao, Neha; Xu, Donghong; Simkins, Tyrell J; Bowles, Owen; Liu, Genzhou; Benattia, Youcef; Griffith, Adrienne; Heitner, Stephen B; Kupfer, Stuart; German, Polina

Characterization and Application of Novel Exercise Recovery Patterns That Reflect Cardiac Performance: A Substudy of the SEQUOIA-HCM Trial

反映心脏功能的新型运动恢复模式的特征分析与应用:SEQUOIA-HCM试验的子研究

Campain, Joseph; Griskowitz, Catharine; Newlands, Chloe; Claggett, Brian L; Kulac, Ian J; McGinnis, Shaina; Giverts, Ilya; Moreno, Fabely; Minasian, Alexandra; Prasad, Cheshta; Rupert, Lillian; Landsteiner, Isabela; Iskenderian, Nick; Coats, Caroline J; Lee, Matthew M Y; Maron, Martin S; Owens, Anjali T; Jacoby, Daniel L; Heitner, Stephen B; Kupfer, Stuart; Malik, Fady I; Wohltman, Amy; Malhotra, Rajeev; Lewis, Gregory D

Cardiac biomarkers and effects of aficamten in obstructive hypertrophic cardiomyopathy: the SEQUOIA-HCM trial

梗阻性肥厚型心肌病患者的心脏生物标志物及阿菲卡明疗效:SEQUOIA-HCM试验

Coats, Caroline J; Masri, Ahmad; Barriales-Villa, Roberto; Abraham, Theodore P; Brinkley, Douglas Marshall; Claggett, Brian L; Hagege, Albert; Hegde, Sheila M; Ho, Carolyn Y; Kulac, Ian J; Lee, Matthew M Y; Maron, Martin S; Olivotto, Iacopo; Owens, Anjali T; Solomon, Scott D; Tfelt-Hansen, Jacob; Watkins, Hugh; Jacoby, Daniel L; Heitner, Stephen B; Kupfer, Stuart; Malik, Fady I; Meng, Lisa; Wohltman, Amy; Januzzi, James L