日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

AAV vectors trigger DNA damage response-dependent pro-inflammatory signalling in human iPSC-derived CNS models and mouse brain

AAV载体在人iPSC衍生的中枢神经系统模型和小鼠脑中触发DNA损伤反应依赖性促炎信号通路。

Costa-Verdera, Helena; Meneghini, Vasco; Fitzpatrick, Zachary; Abou Alezz, Monah; Fabyanic, Emily; Huang, Xin; Dzhashiashvili, Yulia; Ahiya, Avantika; Mangiameli, Elisabeth; Valeri, Erika; Crivicich, Giovanni; Piccolo, Silvia; Cuccovillo, Ivan; Caccia, Roberta; Chan, Ying Kai; Bertin, Bérangère; Ronzitti, Giuseppe; Engel, Esteban A; Merelli, Ivan; Mingozzi, Federico; Gritti, Angela; Kuranda, Klaudia; Kajaste-Rudnitski, Anna

The Influence of Menstrual Cycle Phases on Maximal Strength Performance in Healthy Female Adults: A Systematic Review with Meta-Analysis

月经周期阶段对健康成年女性最大力量表现的影响:系统评价与荟萃分析

Niering, Marc; Wolf-Belala, Nacera; Seifert, Johanna; Tovar, Ole; Coldewey, Jacqueline; Kuranda, Jennifer; Muehlbauer, Thomas

Pre-existing humoral immunity and complement pathway contribute to immunogenicity of adeno-associated virus (AAV) vector in human blood

预先存在的体液免疫和补体途径导致腺相关病毒 (AAV) 载体在人体血液中产生免疫原性

Corinne J Smith, Nikki Ross, Ali Kamal, Kevin Y Kim, Elizabeth Kropf, Pascal Deschatelets, Cedric Francois, William J Quinn 3rd, Inderpal Singh, Anna Majowicz, Federico Mingozzi, Klaudia Kuranda

Early Phase Clinical Immunogenicity of Valoctocogene Roxaparvovec, an AAV5-Mediated Gene Therapy for Hemophilia A

Valoctocogene Roxaparvovec(一种用于治疗血友病A的AAV5介导基因疗法)的早期临床免疫原性研究

Long, Brian R; Veron, Philippe; Kuranda, Klaudia; Hardet, Romain; Mitchell, Nina; Hayes, Gregory M; Wong, Wing Yen; Lau, Kelly; Li, Mingjin; Hock, M Benjamin; Zoog, Stephen J; Vettermann, Christian; Mingozzi, Federico; Schweighardt, Becky

The Effect of CpG Sequences on Capsid-Specific CD8(+) T Cell Responses to AAV Vector Gene Transfer

CpG序列对AAV载体基因转移诱导的衣壳特异性CD8(+) T细胞反应的影响

Xiang, ZhiQuan; Kurupati, Raj K; Li, Yan; Kuranda, Klaudia; Zhou, Xiangyang; Mingozzi, Federico; High, Katherine A; Ertl, Hildegund C J

AAV Vector Immunogenicity in Humans: A Long Journey to Successful Gene Transfer

AAV载体在人体内的免疫原性:基因转移成功的漫长征程

Costa Verdera, Helena; Kuranda, Klaudia; Mingozzi, Federico

Long-Term Follow-Up of the First in Human Intravascular Delivery of AAV for Gene Transfer: AAV2-hFIX16 for Severe Hemophilia B

首次人体血管内递送腺相关病毒(AAV)进行基因转移的长期随访:AAV2-hFIX16 用于治疗重型血友病 B

George, Lindsey A; Ragni, Margaret V; Rasko, John E J; Raffini, Leslie J; Samelson-Jones, Benjamin J; Ozelo, Margareth; Hazbon, Maria; Runowski, Alexa R; Wellman, Jennifer A; Wachtel, Katie; Chen, Yifeng; Anguela, Xavier M; Kuranda, Klaudia; Mingozzi, Federico; High, Katherine A

Islet-reactive CD8(+) T cell frequencies in the pancreas, but not in blood, distinguish type 1 diabetic patients from healthy donors

胰腺中而非血液中胰岛反应性 CD8(+) T 细胞的频率可以区分 1 型糖尿病患者和健康供体。

Culina, Slobodan; Lalanne, Ana Ines; Afonso, Georgia; Cerosaletti, Karen; Pinto, Sheena; Sebastiani, Guido; Kuranda, Klaudia; Nigi, Laura; Eugster, Anne; Østerbye, Thomas; Maugein, Alicia; McLaren, James E; Ladell, Kristin; Larger, Etienne; Beressi, Jean-Paul; Lissina, Anna; Appay, Victor; Davidson, Howard W; Buus, Søren; Price, David A; Kuhn, Matthias; Bonifacio, Ezio; Battaglia, Manuela; Caillat-Zucman, Sophie; Dotta, Francesco; Scharfmann, Raphael; Kyewski, Bruno; Mallone, Roberto

Exposure to wild-type AAV drives distinct capsid immunity profiles in humans

人类接触野生型AAV后会产生不同的衣壳免疫谱。

Klaudia Kuranda ,Priscilla Jean-Alphonse ,Christian Leborgne ,Romain Hardet ,Fanny Collaud ,Solenne Marmier ,Helena Costa Verdera ,Giuseppe Ronzitti ,Philippe Veron ,Federico Mingozzi

Changes in chromatin state reveal ARNT2 at a node of a tumorigenic transcription factor signature driving glioblastoma cell aggressiveness

染色质状态的变化揭示了 ARNT2 位于致瘤转录因子特征节点处,该特征可驱动胶质母细胞瘤细胞侵袭性

Alexandra Bogeas, Ghislaine Morvan-Dubois, Elias A El-Habr, François-Xavier Lejeune, Matthieu Defrance, Ashwin Narayanan, Klaudia Kuranda, Fanny Burel-Vandenbos, Salwa Sayd, Virgile Delaunay, Luiz G Dubois, Hugues Parrinello, Stéphanie Rialle, Sylvie Fabrega, Ahmed Idbaih, Jacques Haiech, Ivan Bièch