Systemic deletion of DMD exon 51 rescues clinically severe Duchenne muscular dystrophy in a pig model lacking DMD exon 52
在缺乏 DMD 外显子 52 的猪模型中,系统性删除 DMD 外显子 51 可挽救临床严重的杜氏肌营养不良症
期刊:Proceedings of the National Academy of Sciences of the United States of America
影响因子:
doi:10.1073/pnas.2301250120
Michael Stirm, Bachuki Shashikadze, Andreas Blutke, Elisabeth Kemter, Andreas Lange, Jan B Stöckl, Florian Jaudas, Laeticia Laane, Mayuko Kurome, Barbara Keßler, Valeri Zakhartchenko, Andrea Bähr, Nikolai Klymiuk, Hiroshi Nagashima, Maggie C Walter, Wolfgang Wurst, Christian Kupatt, Thomas Fröhlich,