In vivo mitochondrial base editing restores genotype and visual function in a mouse model of LHON
体内线粒体碱基编辑可恢复LHON小鼠模型的基因型和视觉功能。
期刊:Nature Communications
影响因子:14.7
doi:10.1038/s41467-025-66600-3.
Sanghun Kim #,Jieun Kim #,Seongkwang Cha #,Sungjin Ju #,Chae Jin Lim #,Seongho Hong,Jiyoung Bae,Yeji Oh,Sungmo Jung,Sol Pin Kim,Hae-Sol Shin,Jae Hee Yoon,Jeeyoon Park,Seungmin Ryou,Soo-Yeon Lim,Su Bin Lee,Seung Hee Choi,Soo-Ji Park,Chang Geun Choi,Mihyun Choi,Lark Kyun Kim,Jiyoon Park,Seonghyun Lee,Kyoung Yul Seo,Je Kyung Seong,Kyoungmi Kim,Jin-Soo Kim,Hyunji Lee