Once-Weekly Navepegritide in Children With Achondroplasia: The APPROACH Randomized Clinical Trial
每周一次使用萘培格里肽治疗软骨发育不全患儿：APPROACH随机临床试验
期刊:Jama Pediatrics
影响因子:18
doi:10.1001/jamapediatrics.2025.4771
Savarirayan, Ravi; McDonnell, Ciara; Bacino, Carlos A; Hoernschemeyer, Daniel G; Legare, Janet M; Abuzzahab, M Jennifer; Hofman, Paul L; Campeau, Philippe M; de Bergua Domingo, Josep Maria; Ward, Leanne M; Smit, Kevin; Smith, Alden; Mao, Meng; Ominsky, Michael S; Freiberg, Lærke C; Shu, Aimee D; Hove, Hanne B
