Pilocytic astrocytoma in a child with spinal muscular atrophy treated with onasemnogene abeparvovec
一名接受onasemnogene abeparvovec治疗的脊髓性肌萎缩症患儿出现毛细胞型星形细胞瘤。
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2025.02.025
Holzwarth, Dorothea; Calaminus, Gabriele; Friese, Johannes; Sejersen, Thomas; Büning, Hildegard; John-Neek, Philipp; Bastone, Antonella Lucía; Rothe, Michael; Mansfield, Keith; Libertini, Silvana; Dubost, Valérie; Kuzmiski, Brent; Alecu, Iulian; Labik, Ivan; Kirschner, Janbernd
