Antibody Therapy Targeting RAN Proteins Rescues C9 ALS/FTD Phenotypes in C9orf72 Mouse Model
针对 RAN 蛋白的抗体疗法可挽救 C9orf72 小鼠模型中的 C9 ALS/FTD 表型
期刊:Neuron
影响因子:14.7
doi:10.1016/j.neuron.2019.11.007
Lien Nguyen, Fabio Montrasio, Amrutha Pattamatta, Solaleh Khoramian Tusi, Olgert Bardhi, Kevin D Meyer, Lindsey Hayes, Katsuya Nakamura, Monica Banez-Coronel, Alyssa Coyne, Shu Guo, Lauren A Laboissonniere, Yuanzheng Gu, Saravanakumar Narayanan, Benjamin Smith, Roger M Nitsch, Mark W Kankel, Mia Rus