Rimeporide as a first- in-class NHE-1 inhibitor: Results of a phase Ib trial in young patients with Duchenne Muscular Dystrophy
利美泊利作为首个同类NHE-1抑制剂:一项针对年轻杜氏肌营养不良症患者的Ib期试验结果
期刊:Pharmacological Research
影响因子:10.5
doi:10.1016/j.phrs.2020.104999
Previtali, Stefano C; Gidaro, Teresa; Díaz-Manera, Jordi; Zambon, Alberto; Carnesecchi, Stephanie; Roux-Lombard, Pascale; Spitali, Pietro; Signorelli, Mirko; Szigyarto, Cristina Al-Khalili; Johansson, Camilla; Gray, Julian; Labolle, Delphine; Porte Thomé, Florence; Pitchforth, Jacqueline; Domingos, Joana; Muntoni, Francesco