CRISPR-targeted genome editing of human induced pluripotent stem cell-derived hepatocytes for the treatment of Wilson's disease
利用CRISPR靶向基因组编辑技术对人诱导多能干细胞衍生的肝细胞进行基因编辑,以治疗威尔逊病
期刊:Jhep Reports
影响因子:7.5
doi:10.1016/j.jhepr.2021.100389
Wei, Rui; Yang, Jiayin; Cheng, Chi-Wa; Ho, Wai-In; Li, Na; Hu, Yang; Hong, Xueyu; Fu, Jian; Yang, Bo; Liu, Yuqing; Jiang, Lixiang; Lai, Wing-Hon; Au, Ka-Wing; Tsang, Wai-Ling; Tse, Yiu-Lam; Ng, Kwong-Man; Esteban, Miguel A; Tse, Hung-Fat