Modeling Human Severe Combined Immunodeficiency and Correction by CRISPR/Cas9-Enhanced Gene Targeting
利用 CRISPR/Cas9 增强型基因靶向技术构建人类重症联合免疫缺陷模型并进行矫正
期刊:Cell Reports
影响因子:6.9
doi:10.1016/j.celrep.2015.08.013
Chang, Chia-Wei; Lai, Yi-Shin; Westin, Erik; Khodadadi-Jamayran, Alireza; Pawlik, Kevin M; Lamb, Lawrence S Jr; Goldman, Frederick D; Townes, Tim M