日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

The Implication of Hinge 1 and Hinge 4 in Micro-Dystrophin Gene Therapy for Duchenne Muscular Dystrophy

铰链 1 和铰链 4 在杜氏肌营养不良症微肌营养不良蛋白基因治疗中的意义

Lakmini P Wasala, Thais B Watkins, Nalinda B Wasala, Matthew J Burke, Yongping Yue, Yi Lai, Gang Yao, Dongsheng Duan

The gRNA Vector Level Determines the Outcome of Systemic AAV CRISPR Therapy for Duchenne Muscular Dystrophy

gRNA 载体水平决定杜氏肌营养不良症系统性 AAV CRISPR 治疗的结果

Nalinda B Wasala, Emily D Million, Thais B Watkins, Lakmini P Wasala, Jin Han, Yongping Yue, Baisong Lu, Shi-Jie Chen, Chady H Hakim, Dongsheng Duan

Single SERCA2a Therapy Ameliorated Dilated Cardiomyopathy for 18 Months in a Mouse Model of Duchenne Muscular Dystrophy

单一 SERCA2a 疗法在杜氏肌营养不良症小鼠模型中改善了扩张型心肌病,持续 18 个月

Nalinda B Wasala, Yongping Yue, William Lostal, Lakmini P Wasala, Nandita Niranjan, Roger J Hajjar, Gopal J Babu, Dongsheng Duan

Micro-dystrophin AAV Vectors Made by Transient Transfection and Herpesvirus System Are Equally Potent in Treating mdx Mouse Muscle Disease

瞬时转染和疱疹病毒系统制备的微肌营养不良蛋白 AAV 载体在治疗 mdx 小鼠肌肉疾病方面同样有效

Chady H Hakim, Nathalie Clément, Lakmini P Wasala, Hsiao T Yang, Yongping Yue, Keqing Zhang, Kasun Kodippili, Laura Adamson-Small, Xiufang Pan, Joel S Schneider, N Nora Yang, Jeffrey S Chamberlain, Barry J Byrne, Dongsheng Duan

Systemic Delivery of Adeno-Associated Viral Vectors in Mice and Dogs

在小鼠和犬体内系统性递送腺相关病毒载体

Wasala, Lakmini P; Hakim, Chady H; Yue, Yongping; Yang, N Nora; Duan, Dongsheng

AAV CRISPR editing rescues cardiac and muscle function for 18 months in dystrophic mice

AAV CRISPR 编辑挽救了营养不良小鼠 18 个月的心脏和肌肉功能

Chady H Hakim, Nalinda B Wasala, Christopher E Nelson, Lakmini P Wasala, Yongping Yue, Jacqueline A Louderman, Thais B Lessa, Aihua Dai, Keqing Zhang, Gregory J Jenkins, Michael E Nance, Xiufang Pan, Kasun Kodippili, N Nora Yang, Shi-Jie Chen, Charles A Gersbach, Dongsheng Duan

Cryptococcal meningitis presenting with bilateral complete ophthalmoplegia: a case report

隐球菌性脑膜炎伴双侧完全性眼肌麻痹:病例报告

Liyanage, Damith S; Pathberiya, Lakmini P S; Gooneratne, Inuka K; Caldera, Manjula H P C; Perera, Priyankara W S; Gamage, Ranjani