AAV CRISPR editing rescues cardiac and muscle function for 18 months in dystrophic mice
AAV CRISPR 编辑挽救了营养不良小鼠 18 个月的心脏和肌肉功能
期刊:JCI Insight
影响因子:6.3
doi:10.1172/jci.insight.124297
Chady H Hakim, Nalinda B Wasala, Christopher E Nelson, Lakmini P Wasala, Yongping Yue, Jacqueline A Louderman, Thais B Lessa, Aihua Dai, Keqing Zhang, Gregory J Jenkins, Michael E Nance, Xiufang Pan, Kasun Kodippili, N Nora Yang, Shi-Jie Chen, Charles A Gersbach, Dongsheng Duan