Human stem cell-based retina on chip as new translational model for validation of AAV retinal gene therapy vectors
基于人类干细胞的视网膜芯片作为验证 AAV 视网膜基因治疗载体的新转化模型
期刊:Stem Cell Reports
影响因子:5.9
doi:10.1016/j.stemcr.2021.08.008
Kevin Achberger, Madalena Cipriano, Matthias J Düchs, Christian Schön, Stefan Michelfelder, Birgit Stierstorfer, Thorsten Lamla, Stefan G Kauschke, Johanna Chuchuy, Julia Roosz, Lena Mesch, Virginia Cora, Selin Pars, Natalia Pashkovskaia, Serena Corti, Sophia-Marie Hartmann, Alexander Kleger, Sebast