CRISPR-Cas9-mediated homology-directed repair rescues the induced bone marrow failure in Fancc (-/-) mice
CRISPR-Cas9介导的同源定向修复可挽救Fancc(-/-)小鼠的诱导性骨髓衰竭。
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.1
doi:10.1016/j.omtn.2026.102912
Harikrishnan, Hemavathy; Lamsal, Mahesh; Chan, Ka-Kui; Zhang, Junping; Tian, Jiahe; Fosu, Kwadwo; Nguyen, Hong Phuong; Clapp, D Wade; Sierra Potchanant, Elizabeth A; Kapur, Reuben; Xiao, Weidong; Tran, Ngoc Tung