日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Agreement Between Child Self- and Parent Proxy-Reports of Health-Related Quality of Life in Spinal Muscular Atrophy: Preliminary Insights from a Nationwide Patient Registry in Germany

德国全国患者登记研究初步揭示了脊髓性肌萎缩症患者健康相关生活质量的儿童自述报告与父母代理报告之间的一致性

Landfeldt, Erik; Leibrock, Berenike; Hussong, Justine; Thiele, Simone; Walter, Maggie C; Moehler, Eva; Zemlin, Michael; Dillmann, Ulrich; Flotats-Bastardas, Marina

Real-world clinical outcomes of patients with high-risk endometrial cancer or endometrial carcinosarcoma in England: A retrospective cohort study

英格兰高危子宫内膜癌或子宫内膜癌肉瘤患者的真实世界临床结局:一项回顾性队列研究

Prabhu, Vimalanand S; Landfeldt, Erik; Ralphs, Eleanor; Teoh, Cheryl; Ridsdale-Smith, Jess; Macey, Karen; Trankov, Nikolay; Lambova, Alexandrina; Lichfield, Jasmine; Eminowicz, Gemma

Overall Survival of Patients With Pyruvate Kinase Deficiency in the UK: A Real-World Study

英国丙酮酸激酶缺乏症患者的总体生存率:一项真实世界研究

Foy, Patrick; Higa, Sara; Zhao, Jing; Keapoletswe, Karabo; Cirneanu, Lorena; Venerus, Alessandra; Raiteri, Louise; Landfeldt, Erik; Iob, Eleonora; Lombard, Louise; Li, Junlong; Zagadailov, Erin

Predictors of cardiac disease in duchenne muscular dystrophy: a systematic review and evidence grading

杜氏肌营养不良症心脏疾病的预测因素:系统评价和证据分级

Landfeldt, Erik; Alemán, Alberto; Abner, Sophia; Zhang, Rongrong; Werner, Christian; Tomazos, Ioannis; Lochmüller, Hanns; Quinlivan, Ros M; Wahbi, Karim

Predictors of Loss of Ambulation in Duchenne Muscular Dystrophy: A Systematic Review and Meta-Analysis

杜氏肌营养不良症患者丧失行走能力的预测因素:系统评价和荟萃分析

Landfeldt, E; Alemán, A; Abner, S; Zhang, R; Werner, C; Tomazos, I; Ferizovic, N; Lochmüller, H; Kirschner, J

Factors Associated with Respiratory Health and Function in Duchenne Muscular Dystrophy: A Systematic Review and Evidence Grading

杜氏肌营养不良症患者呼吸健康和功能相关因素:系统评价和证据分级

Landfeldt, E; Aleman, A; Abner, S; Zhang, R; Werner, C; Tomazos, I; Lochmüller, H; Quinlivan, R M

Areas of improvement in the medical care of SMA: evidence from a nationwide patient registry in Germany

德国全国患者登记研究揭示了脊髓性肌萎缩症(SMA)医疗护理中需要改进的领域:证据

Leibrock, Berenike; Landfeldt, Erik; Hussong, Justine; Huelle, Tabea; Mattheus, Hannah; Thiele, Simone; Walter, Maggie C; Zemlin, Michael; Moehler, Eva; Dillman, Ullrich; Abner, Sophia; Flotats-Bastardas, Marina

Lifetime impact of achondroplasia study in Europe (LIAISE): findings from a multinational observational study

欧洲软骨发育不全终生影响研究(LIAISE):一项多国观察性研究的发现

Maghnie, Mohamad; Semler, Oliver; Guillen-Navarro, Encarna; Selicorni, Angelo; Heath, Karen E; Haeusler, Gabriele; Hagenäs, Lars; Merker, Andrea; Leiva-Gea, Antonio; González, Vanesa López; Raimann, Adalbert; Rehberg, Mirko; Santos-Simarro, Fernando; Ertl, Diana-Alexandra; Gregersen, Pernille Axél; Onesimo, Roberta; Landfeldt, Erik; Jarrett, James; Quinn, Jennifer; Rowell, Richard; Pimenta, Jeanne; Cohen, Shelda; Butt, Thomas; Shediac, Renée; Mukherjee, Swati; Mohnike, Klaus

Gene Therapy for Neuromuscular Diseases: Health Economic Challenges and Future Perspectives

神经肌肉疾病的基因治疗:卫生经济学挑战和未来展望

Landfeldt, Erik

Costs of Illness of Spinal Muscular Atrophy: A Systematic Review

脊髓性肌萎缩症的疾病成本:系统性综述

Landfeldt, Erik; Pechmann, Astrid; McMillan, Hugh J; Lochmüller, Hanns; Sejersen, Thomas