日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Safety and tolerability of tegoprubart in patients with amyotrophic lateral sclerosis: A Phase 2A clinical trial.

替戈普鲁巴特治疗肌萎缩侧索硬化症患者的安全性和耐受性:一项 2A 期临床试验

Perrin Steven, Ladha Shafeeq, Maragakis Nicholas, Rivner Michael H, Katz Jonathan, Genge Angela, Olney Nicholas, Lange Dale, Heitzman Daragh, Bodkin Cynthia, Jawdat Omar, Goyal Namita A, Bornstein Jeffrey D, Mak Carmen, Appel Stanley H, Paganoni Sabrina

Effect of Ezogabine on Cortical and Spinal Motor Neuron Excitability in Amyotrophic Lateral Sclerosis: A Randomized Clinical Trial

依佐加宾对肌萎缩侧索硬化症皮质和脊髓运动神经元兴奋性的影响:一项随机临床试验

Wainger, Brian J; Macklin, Eric A; Vucic, Steve; McIlduff, Courtney E; Paganoni, Sabrina; Maragakis, Nicholas J; Bedlack, Richard; Goyal, Namita A; Rutkove, Seward B; Lange, Dale J; Rivner, Michael H; Goutman, Stephen A; Ladha, Shafeeq S; Mauricio, Elizabeth A; Baloh, Robert H; Simmons, Zachary; Pothier, Lindsay; Kassis, Sylvia Baedorf; La, Thuong; Hall, Meghan; Evora, Armineuza; Klements, David; Hurtado, Aura; Pereira, Joao D; Koh, Joan; Celnik, Pablo A; Chaudhry, Vinay; Gable, Karissa; Juel, Vern C; Phielipp, Nicolas; Marei, Adel; Rosenquist, Peter; Meehan, Sean; Oskarsson, Björn; Lewis, Richard A; Kaur, Divpreet; Kiskinis, Evangelos; Woolf, Clifford J; Eggan, Kevin; Weiss, Michael D; Berry, James D; David, William S; Davila-Perez, Paula; Camprodon, Joan A; Pascual-Leone, Alvaro; Kiernan, Matthew C; Shefner, Jeremy M; Atassi, Nazem; Cudkowicz, Merit E

Clinical Effects of the Self-administered Subcutaneous Complement Inhibitor Zilucoplan in Patients With Moderate to Severe Generalized Myasthenia Gravis: Results of a Phase 2 Randomized, Double-Blind, Placebo-Controlled, Multicenter Clinical Trial

自我注射皮下补体抑制剂齐鲁普兰治疗中重度全身型重症肌无力患者的临床疗效:一项 II 期随机、双盲、安慰剂对照、多中心临床试验的结果

Howard, James F Jr; Nowak, Richard J; Wolfe, Gil I; Freimer, Miriam L; Vu, Tuan H; Hinton, John L; Benatar, Michael; Duda, Petra W; MacDougall, James E; Farzaneh-Far, Ramin; Kaminski, Henry J; Barohn, Richard; Dimachkie, Mazen; Pasnoor, Mamatha; Farmakidis, Constantine; Liu, Tina; Colgan, Samantha; Benatar, Michael G; Bertorini, Tulio; Pillai, Rekha; Henegar, Robert; Bromberg, Mark; Gibson, Summer; Janecki, Teresa; Freimer, Miriam; Elsheikh, Bakri; Matisak, Paige; Genge, Angela; Guidon, Amanda; David, William; Habib, Ali A; Mathew, Veena; Mozaffar, Tahseen; Hinton, John L; Hewitt, William; Barnett, Deborah; Sullivan, Patricia; Ho, Doreen; Howard, James F Jr; Traub, Rebecca E; Chopra, Manisha; Kaminski, Henry J; Aly, Radwa; Bayat, Elham; Abu-Rub, Mohammad; Khan, Shaida; Lange, Dale; Holzberg, Shara; Khatri, Bhupendra; Lindman, Emily; Olapo, Tayo; Sershon, Lisa M; Lisak, Robert P; Bernitsas, Evanthia; Jia, Kelly; Malik, Rabia; Lewis-Collins, Tiffany D; Nicolle, Michael; Nowak, Richard J; Sharma, Aditi; Roy, Bhaskar; Nye, Joan; Pulley, Michael; Berger, Alan; Shabbir, Yasmeen; Sachdev, Amit; Patterson, Kimberly; Siddiqi, Zaeem; Sivak, Mark; Bratton, Joan; Small, George; Kohli, Anem; Fetter, Mary; Vu, Tuan; Lam, Lucy; Harvey, Brittany; Wolfe, Gil I; Silvestri, Nicholas; Patrick, Kara; Zakalik, Karen; Duda, Petra W; MacDougall, James; Farzaneh-Far, Ramin; Pontius, Angela; Hoarty, Michelle

Clinical care and therapeutic trials in PLS

PLS的临床护理和治疗试验

Floeter, Mary Kay; Warden, Deborah; Lange, Dale; Wymer, James; Paganoni, Sabrina; Mitsumoto, Hiroshi

Pyrimethamine significantly lowers cerebrospinal fluid Cu/Zn superoxide dismutase in amyotrophic lateral sclerosis patients with SOD1 mutations

乙胺嘧啶可显著降低携带SOD1突变的肌萎缩侧索硬化症患者的脑脊液中Cu/Zn超氧化物歧化酶水平。

Lange, Dale J; Shahbazi, Mona; Silani, Vincenzo; Ludolph, Albert C; Weishaupt, Jochen H; Ajroud-Driss, Senda; Fields, Kara G; Remanan, Rahul; Appel, Stanley H; Morelli, Claudia; Doretti, Alberto; Maderna, Luca; Messina, Stefano; Weiland, Ulrike; Marklund, Stefan L; Andersen, Peter M

Quantitative susceptibility mapping of the motor cortex in amyotrophic lateral sclerosis and primary lateral sclerosis

肌萎缩侧索硬化症和原发性侧索硬化症运动皮层的定量磁化率成像

Schweitzer, Andrew D; Liu, Tian; Gupta, Ajay; Zheng, Karen; Seedial, Stephen; Shtilbans, Alexander; Shahbazi, Mona; Lange, Dale; Wang, Yi; Tsiouris, A John

Safety, pharmacokinetic, and functional effects of the nogo-a monoclonal antibody in amyotrophic lateral sclerosis: a randomized, first-in-human clinical trial

nogo-a单克隆抗体在肌萎缩侧索硬化症中的安全性、药代动力学和功能效应:一项随机、首次人体临床试验

Meininger, Vincent; Pradat, Pierre-François; Corse, Andrea; Al-Sarraj, Safa; Rix Brooks, Benjamin; Caress, James B; Cudkowicz, Merit; Kolb, Stephen J; Lange, Dale; Leigh, P Nigel; Meyer, Thomas; Milleri, Stefano; Morrison, Karen E; Orrell, Richard W; Peters, Gary; Rothstein, Jeffrey D; Shefner, Jeremy; Lavrov, Arseniy; Williams, Nicola; Overend, Phil; Price, Jeffrey; Bates, Stewart; Bullman, Jonathan; Krull, David; Berges, Alienor; Abila, Bams; Meno-Tetang, Guy; Wurthner, Jens

Vgf is a novel biomarker associated with muscle weakness in amyotrophic lateral sclerosis (ALS), with a potential role in disease pathogenesis

VGF是一种与肌萎缩侧索硬化症(ALS)肌肉无力相关的新型生物标志物,可能在疾病发病机制中发挥作用。

Zhao, Zhong; Lange, Dale J; Ho, Lap; Bonini, Sara; Shao, Belinda; Salton, Stephen R; Thomas, Sunil; Pasinetti, Giulio Maria

A ketogenic diet as a potential novel therapeutic intervention in amyotrophic lateral sclerosis

生酮饮食作为肌萎缩侧索硬化症的一种潜在新型治疗干预措施

Zhao, Zhong; Lange, Dale J; Voustianiouk, Andrei; MacGrogan, Donal; Ho, Lap; Suh, Jason; Humala, Nelson; Thiyagarajan, Meenakshisundaram; Wang, Jun; Pasinetti, Giulio M