Stereochemistry Enhances Potency, Efficacy, and Durability of Malat1 Antisense Oligonucleotides In Vitro and In Vivo in Multiple Species
立体化学增强了Malat1反义寡核苷酸在体外和体内多种物种中的效力、功效和持久性
期刊:Translational Vision Science & Technology
影响因子:2.6
doi:10.1167/tvst.10.1.23
Byrne, Michael; Vathipadiekal, Vinod; Apponi, Luciano; Iwamoto, Naoki; Kandasamy, Pachamuthu; Longo, Kenneth; Liu, Fangjun; Looby, Richard; Norwood, Lauren; Shah, Anee; Shelke, Juili Dilip; Shivalila, Chikdu; Yang, Hailin; Yin, Yuan; Guo, Lankai; Bowman, Keith; Vargeese, Chandra