Antisense oligonucleotides to KIF1A polymorphisms expand targets and rescue patient-derived neurons in vitro.
针对 KIF1A 多态性的反义寡核苷酸可以扩大靶点，并在体外挽救患者来源的神经元。
期刊:Nature Communications
影响因子:15.7
doi:10.1038/s41467-025-67752-y
Zuccaro Michael V, Young Randee E, Hu Jiangyuan, Lanzano Patricia, Semenova Ekaterina, Lin Xiaoqi, Skowronski Alicja, Shen Yufeng, Kim Tae Hyun, Miller Danny E, Germain Noelle, Sarmiere Patrick, LeDuc Charles A, Chung Wendy K
