STEM-PD trial protocol: a multi-centre, single-arm, first-in-human, dose-escalation trial, investigating the safety and tolerability of intraputamenal transplantation of human embryonic stem cell-derived dopaminergic cells for Parkinson's disease
STEM-PD试验方案:一项多中心、单组、首次人体剂量递增试验,旨在研究壳核内移植人胚胎干细胞衍生多巴胺能细胞治疗帕金森病的安全性和耐受性。
期刊:BMJ Open
影响因子:2.3
doi:10.1136/bmjopen-2025-107597
Paul, Gesine; Bjartmarz, Hjalmar; Björklund, Anders; Cutting, Emma; Evans, Amy; Harry, Bronwen; Hansson, Oskar; Kayhanian, Saeed; Kirkeby, Agnete; Lao-Kim, Nicholas; Lindvall, Olle; Nelander, Jenny; Piccini, Paola; Smith, Ruben; Ullén, Susann; Van Vliet, Trinette; Widner, Hakan; Parmar, Malin; Barker, Roger A