日期 影响因子
日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:
–

A computational tool to optimize clinical trial parameter selection in Duchenne muscular dystrophy: A practical guide and case studies

用于优化杜氏肌营养不良症临床试验参数选择的计算工具：实用指南和案例研究

期刊:Cpt-Pharmacometrics & Systems Pharmacology
影响因子:3
doi:10.1002/psp4.13281
Wilk, Jordan; Aggarwal, Varun; Pauley, Mike; Corey, Diane; Conrado, Daniela J; Lingineni, Karthik; Morales, Juan Francisco; Yoon, Deok Yong; Zhang, Yi; Cui, Zihan; Burton, Jackson; Larkindale, Jane; Ma, Shu Chin; Hovinga, Collin; Martinez, Terina; Romero, Klaus; Belfiore-Oshan, Ramona; Kim, Sarah
发表日期：2025
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Correction: Developing a Natural History Model for Duchenne Muscular Dystrophy

更正：建立杜氏肌营养不良症的自然史模型

期刊:Pharmacoeconomics-Open
影响因子:2.1
doi:10.1007/s41669-024-00506-6
Broomfield, Jonathan; Hill, M; Chandler, F; Crowther, M J; Godfrey, J; Guglieri, M; Hastie, J; Larkindale, J; Mumby-Croft, J; Reuben, E; Woodcock, F; Abrams, K R
发表日期：2024
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Developing a Natural History Model for Duchenne Muscular Dystrophy

建立杜氏肌营养不良症的自然史模型

期刊:Pharmacoeconomics-Open
影响因子:2.1
doi:10.1007/s41669-023-00450-x
Broomfield, Jonathan; Hill, M; Chandler, F; Crowther, M J; Godfrey, J; Guglieri, M; Hastie, J; Larkindale, J; Mumby-Croft, J; Reuben, E; Woodcock, F; Abrams, K R
发表日期：2024
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Patient-Reported Impact of Symptoms in Friedreich Ataxia

弗里德赖希共济失调患者报告的症状影响

期刊:Neurology
影响因子:8.5
doi:10.1212/WNL.0000000000201598
Seabury, Jamison; Alexandrou, Danae; Dilek, Nuran; Cohen, Brittany; Heatwole, John; Larkindale, Jane; Lynch, David R; Park, Courtney; Rosero, Spencer; Subramony, Sub H; Varma, Anika; Wagner, Ellen; Walther, Susan; Weinstein, Jennifer; Wells, McKenzie; Zizzi, Christine; Heatwole, Chad
发表日期：2023
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Friedreich's Ataxia-Health Index: Development and Validation of a Novel Disease-Specific Patient-Reported Outcome Measure

弗里德赖希共济失调健康指数：一种新型疾病特异性患者报告结局指标的开发与验证

期刊:Neurology-Clinical Practice
影响因子:3.2
doi:10.1212/CPJ.0000000000200180
Seabury, Jamison; Rosero, Spencer; Varma, Anika; Weinstein, Jennifer; Engebrecht, Charlotte; Dilek, Nuran; Heatwole, John; Alexandrou, Danae; Cohen, Brittany; Larkindale, Jane; Lynch, David R; Park, Courtney; Subramony, Sub H; Wagner, Ellen; Walther, Susan; Wells, McKenzie; Zizzi, Christine; Heatwole, Chad
发表日期：2023
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The IRDiRC Chrysalis Task Force: making rare disease research attractive to companies

IRDiRC Chrysalis 工作组：使罕见病研究对企业更具吸引力

期刊:Therapeutic Advances in Rare Disease
影响因子:
doi:10.1177/26330040231188979
Beaverson, Katherine L; Julkowska, Daria; Letinturier, Mary Catherine V; Aartsma-Rus, Annemieke; Austin, Jennifer; Bueren, Juan; Frost, Simon; Hamamura, Misako; Larkindale, Jane; LaRosa, Greg; Magenheim, Rita; Merico, Annamaria; Pasmooij, Anna Maria Gerdina; Pirard, Vinciane; Ekow Thomford, Nicholas; Wada, Michihiko; Wong-Rieger, Durhane; Hartman, Adam L
发表日期：2023
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Development of a model-based clinical trial simulation platform to optimize the design of clinical trials for Duchenne muscular dystrophy

开发基于模型的临床试验模拟平台，以优化杜氏肌营养不良症临床试验的设计

期刊:Cpt-Pharmacometrics & Systems Pharmacology
影响因子:3
doi:10.1002/psp4.12753
Lingineni, Karthik; Aggarwal, Varun; Morales, Juan Francisco; Conrado, Daniela J; Corey, Diane; Vong, Camille; Burton, Jackson; Larkindale, Jane; Romero, Klaus; Schmidt, Stephan; Kim, Sarah
发表日期：2022
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Standardized Data Structures in Rare Diseases: CDISC User Guides for Duchenne Muscular Dystrophy and Huntington's Disease

罕见病标准化数据结构：杜氏肌营养不良症和亨廷顿病的 CDISC 用户指南

期刊:Cts-Clinical and Translational Science
影响因子:2.8
doi:10.1111/cts.12845
Mullin, Ariana P; Corey, Diane; Turner, Emily C; Liwski, Richard; Olson, Daniel; Burton, Jackson; Sivakumaran, Sudhir; Hudson, Lynn D; Romero, Klaus; Stephenson, Diane T; Larkindale, Jane
发表日期：2021
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Effective Data Sharing as a Conduit for Advancing Medical Product Development

有效的数据共享是推进医疗产品开发的渠道

期刊:
影响因子:
doi:10.1007/s43441-020-00255-8
Karpen, Stephen R; White, J Kael; Mullin, Ariana P; O'Doherty, Inish; Hudson, Lynn D; Romero, Klaus; Sivakumaran, Sudhir; Stephenson, Diane; Turner, Emily C; Larkindale, Jane
发表日期：2021
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Measuring peripheral nerve involvement in Friedreich's ataxia

测量弗里德赖希共济失调的周围神经受累情况

期刊:Annals of Clinical and Translational Neurology
影响因子:3.9
doi:10.1002/acn3.50865
Creigh, Peter D; Mountain, Joan; Sowden, Janet E; Eichinger, Katy; Ravina, Bernard; Larkindale, Jane; Herrmann, David N
发表日期：2019
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