Drug Candidate BIO101 for Spinal Muscular Atrophy as Monotherapy or Combined With the Antisense Oligonucleotide ASO-10-27
用于治疗脊髓性肌萎缩症的候选药物 BIO101 可作为单药疗法或与反义寡核苷酸 ASO-10-27 联合使用
期刊:Journal of Cachexia Sarcopenia and Muscle
影响因子:9.1
doi:10.1002/jcsm.70104
Bézier, Cynthia; Cottin, Steve; Hashemi, Parvin Nazari; El Khoury, Mirella; Clerc, Zoé; Balducci, Christine; Sapaly, Delphine; Weill, Laure; Lafont, René; Veillet, Stanislas; Dilda, Pierre J; Charbonnier, Frédéric; Latil, Mathilde; Biondi, Olivier