Micro-dystrophin AAV Vectors Made by Transient Transfection and Herpesvirus System Are Equally Potent in Treating mdx Mouse Muscle Disease
瞬时转染和疱疹病毒系统制备的微肌营养不良蛋白 AAV 载体在治疗 mdx 小鼠肌肉疾病方面同样有效
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:
doi:10.1016/j.omtm.2020.07.004
Chady H Hakim, Nathalie Clément, Lakmini P Wasala, Hsiao T Yang, Yongping Yue, Keqing Zhang, Kasun Kodippili, Laura Adamson-Small, Xiufang Pan, Joel S Schneider, N Nora Yang, Jeffrey S Chamberlain, Barry J Byrne, Dongsheng Duan