Design of a Randomized, Placebo-Controlled, Phase 3 Trial of Tofersen Initiated in Clinically Presymptomatic SOD1 Variant Carriers: the ATLAS Study
一项针对临床无症状SOD1变异携带者的Tofersen随机、安慰剂对照3期临床试验的设计:ATLAS研究
期刊:Neurotherapeutics
影响因子:6.9
doi:10.1007/s13311-022-01237-4
Benatar, Michael; Wuu, Joanne; Andersen, Peter M; Bucelli, Robert C; Andrews, Jinsy A; Otto, Markus; Farahany, Nita A; Harrington, Elizabeth A; Chen, Weiping; Mitchell, Adele A; Ferguson, Toby; Chew, Sheena; Gedney, Liz; Oakley, Sue; Heo, Jeong; Chary, Sowmya; Fanning, Laura; Graham, Danielle; Sun, Peng; Liu, Yingying; Wong, Janice; Fradette, Stephanie