日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

IgM Anti-Ganglioside Binding and Complement Activation in an iPSC-Derived Motor Neuron Model for Multifocal Motor Neuropathy

在iPSC衍生运动神经元模型中,IgM抗神经节苷脂结合和补体激活在多灶性运动神经病中的作用

Krijgsman, Daniëlle; Dijkxhoorn, Kim; de Zeeuw, Elisabeth; Bloemenkamp, Lauri M; Bos, Jeroen W; van Eijk, Ruben P A; Van de Walle, Inge; Huizinga, Ruth; Jacobs, Bart C; Leusen, Jeanette H W; Pasterkamp, R Jeroen; Hack, C Erik; Budding, Kevin; van der Pol, W Ludo

Outcomes following matched sibling donor transplantation for severe combined immunodeficiency: a report from the PIDTC

同胞相合供体移植治疗重症联合免疫缺陷的疗效:来自PIDTC的报告

Rayes, Ahmad; Logan, Brent R; Liu, Xuerong; Dara, Jasmeen; Buckley, Rebecca H; Oved, Joseph H; Kapoor, Neena; Kapadia, Malika; Chandra, Sharat; Martinez, Caridad A; Bunin, Nancy J; Chandrakasan, Shanmuganathan; Chen, Karin; Bednarski, Jeffrey J; Haines, Hilary L; Eissa, Hesham; Talano, Julie-An M; Keller, Michael D; Ebens, Christen L; Chaudhury, Sonali; Shereck, Evan B; Aquino, Victor M; Knutsen, Alan P; Alexander, Jessie L; Gillio, Alfred P; Chellapandian, Deepakbabu; Shah, Ami J; Miller, Holly K; Vander Lugt, Mark T; Seroogy, Christine M; Dorsey, Morna J; Mousallem, Talal; Parrott, Roberta E; O'Reilly, Richard J; Aguayo-Hiraldo, Paibel I; Prockop, Susan E; Dávila Saldaña, Blachy J; Thakar, Monica S; Burroughs, Lauri M; Torgerson, Troy R; Leiding, Jennifer W; Marsh, Rebecca A; Griffith, Linda M; Pulsipher, Michael A; Kohn, Donald B; Notarangelo, Luigi; Cowan, Morton J; Puck, Jennifer M; Cuvelier, Geoffrey D E; Heimall, Jennifer; Haddad, Elie; Pai, Sung-Yun; Dvorak, Christopher C

Hematopoietic cell transplantation for Wiskott-Aldrich syndrome: a PIDTC report

造血干细胞移植治疗威斯科特-奥尔德里奇综合征:PIDTC报告

Alexander, Jessie L; Dávila Saldaña, Blachy J; Brazauskas, Ruta; Dammalapati, Sravya Gethika; Griffith, Linda M; Shah, Ami J; Shimano, Kristin A; Ochs, Hans D; Bleesing, Jack J; Ebens, Christen L; Kapadia, Malika; Bauchat, Andrea; Kapoor, Neena; Oved, Joseph H; Eissa, Hesham; Lust, Hannah; Keller, Michael D; Haines, Hilary; Chandrakasan, Shanmuganathan; Talano, Julie-An; Rayes, Ahmad; Madden, Lisa; Shereck, Evan; Miller, Holly K; Satter, Lisa Forbes; Martinez, Caridad; Rozmus, Jacob; Bednarski, Jeffrey J; Yu, Lolie C; Chellapandian, Deepakbabu; Aquino, Victor M; Knutsen, Alan; Chong, Hey; Chopek, Ashley; Gillio, Alfred P; Joshi, Avni; Rangarajan, Hemalatha; Moore, Theodore B; Andolina, Jeffrey R; DeSantes, Kenneth B; Vander Lugt, Mark; Prockop, Susan E; Shyr, David C; Sullivan, Kathleen E; Parikh, Suhag; Weinacht, Katja G; Torgerson, Troy R; Marsh, Rebecca; Dvorak, Christopher C; Chan, Alice Y; Haddad, Elie; Heimall, Jennifer R; Pulsipher, Michael A; Leiding, Jennifer W; Kohn, Donald B; Puck, Jennifer M; Notarangelo, Luigi D; Rawlings, David J; Cowan, Morton J; Petrovic, Aleksandra; Pai, Sung-Yun; Burroughs, Lauri M

Clinical spectrum of Wiskott-Aldrich syndrome carriers: Self-reported survey of 193 carriers

Wiskott-Aldrich综合征携带者的临床表现谱:193名携带者的自我报告调查

Chandrakasan, Shanmuganathan; Westbrook, Adrianna; Griffith, Linda M; Hagin, David; Iyengar, Sumathi; Mangurian, Christina; Scalchunes, Chris; Sullivan, Kathleen E; Zablocki, Akiva; Bakshi, Nitya; Sinha, Cynthia; Burroughs, Lauri M; Chan, Alice Y; Dvorak, Christopher C; Haddad, Elie; Heimall, Jennifer; Kohn, Donald B; Leiding, Jennifer W; Notarangelo, Luigi D; Pai, Sung-Yun; Puck, Jennifer M; Pulsipher, Michael A; Marsh, Rebecca A; Torgerson, Troy; Cowan, Morton J; Ochs, Hans D; Parikh, Suhag

Childbirth Experiences in the United Kingdom Compared to the Netherlands: A Cross-Sectional Survey Study

英国与荷兰分娩经历的比较:一项横断面调查研究

van den Berg, Lauri M M; Henrichs, Jens; van Dillen, Jeroen; Downe, Soo; Verhoeven, Corine; de Jonge, Ank

Allogeneic hematopoietic stem cell transplantation for STAT3 hyper-IgE syndrome: a worldwide study

异基因造血干细胞移植治疗STAT3高IgE综合征:一项全球性研究

Tsilifis, Christo; Raedler, Johannes; Renke, Joanna; Medinger, Michael; Laberko, Alexandra; Haraldsson, Ásgeir; Patel, Niraj; Ciznar, Peter; Wong, Melanie; Keogh, Steven J; Gray, Paul; Mitchell, Richard; Bigley, Venetia; Elcombe, Suzanne; Hauck, Fabian; Albert, Michael H; Tholouli, Eleni; Herwadkar, Archana; Elkhalifa, Shuayb; Kosmidis, Chris; Callisti, Giorgio; Burroughs, Lauri M; Chen, Karin; Carpenter, Ben; Fox, Thomas A; Morris, Emma C; Uppuluri, Ramya; Raj, Revathi; Yanagimachi, Masakatsu; Buddingh, Emilie P; Oikonomopoulou, Christina; Gonzalez, Corina; Dimitrova, Dimana; Kanakry, Jennifer A; Arnold, Danielle; Pai, Sung-Yun; Slatter, Mary A; Pearce, Mark S; Worth, Austen; Freeman, Alexandra F; Gennery, Andrew R

Complement activation by IgM autoantibodies linked to immune-mediated neuropathies depends on C2

与免疫介导性神经病变相关的IgM自身抗体激活补体依赖于C2。

Budding, Kevin; Dijkxhoorn, Kim; de Zeeuw, Elisabeth; Bloemenkamp, Lauri M; van der Pol, W Ludo; Notermans, Nicolette C; Minnema, Monique C; Leusen, Jeanette H W; Hack, C Erik; Van de Walle, Inge

Communication Strategies for Tick-Borne Disease Prevention Among US Cattle Producers: Quasi-Experimental Study on Message Framing and Source Credibility

美国养牛户蜱传疾病预防沟通策略:信息框架和信息源可信度的准实验研究

Yang, Cheng-Xian; Baker, Lauri M; Czipulis, Jessica

Parent's Perspective on Continuity of Care in the Maternity Care and Child Health Services Continuum: A Qualitative Systematic Review

父母对孕产妇保健和儿童保健服务连续性的看法:一项定性系统评价

Hermans, Anne C M; Boertien, Silke; van den Berg, Lauri M M; de Jonge, Ank; Janssen, Danielle E M C; Franx, Arie; van der Kooy, Jacoba; de Kroon, Marlou L A

Posttransplantation late complications increase over time for patients with SCID: A Primary Immune Deficiency Treatment Consortium (PIDTC) landmark study

移植后晚期并发症在重症联合免疫缺陷病(SCID)患者中随时间推移而增加:一项原发性免疫缺陷治疗联盟(PIDTC)里程碑式研究

Eissa, Hesham; Thakar, Monica S; Shah, Ami J; Logan, Brent R; Griffith, Linda M; Dong, Huaying; Parrott, Roberta E; O'Reilly, Richard J; Dara, Jasmeen; Kapoor, Neena; Forbes Satter, Lisa; Chandra, Sharat; Kapadia, Malika; Chandrakasan, Shanmuganathan; Knutsen, Alan; Jyonouchi, Soma C; Molinari, Lyndsay; Rayes, Ahmad; Ebens, Christen L; Teira, Pierre; Dávila Saldaña, Blachy J; Burroughs, Lauri M; Chaudhury, Sonali; Chellapandian, Deepak; Gillio, Alfred P; Goldman, Fredrick; Malech, Harry L; DeSantes, Kenneth; Cuvelier, Geoff D E; Rozmus, Jacob; Quinones, Ralph; Yu, Lolie C; Broglie, Larisa; Aquino, Victor; Shereck, Evan; Moore, Theodore B; Vander Lugt, Mark T; Mousallem, Talal I; Oved, Joeseph H; Dorsey, Morna; Abdel-Azim, Hisham; Martinez, Caridad; Bleesing, Jacob H; Prockop, Susan; Kohn, Donald B; Bednarski, Jeffrey J; Leiding, Jennifer; Marsh, Rebecca A; Torgerson, Troy; Notarangelo, Luigi D; Pai, Sung-Yun; Pulsipher, Michael A; Puck, Jennifer M; Dvorak, Christopher C; Haddad, Elie; Buckley, Rebecca H; Cowan, Morton J; Heimall, Jennifer