日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Small-Molecule PAPD5 Inhibitors Restore Telomerase Activity in Patient Stem Cells

小分子PAPD5抑制剂可恢复患者干细胞中的端粒酶活性

Neha Nagpal ,Jianing Wang ,Jing Zeng ,Emily Lo ,Diane H Moon ,Kevin Luk ,Roman O Braun ,Lauri M Burroughs ,Sioban B Keel ,Christopher Reilly ,R Coleman Lindsley ,Scot A Wolfe ,Albert K Tai ,Patrick Cahan ,Daniel E Bauer ,Yick W Fong ,Suneet Agarwal

Novel lineage depletion preserves autologous blood stem cells for gene therapy of Fanconi anemia complementation group A

新型谱系耗竭技术保留自体血液干细胞用于范可尼贫血互补组 A 的基因治疗

Jennifer E Adair, Devikha Chandrasekaran, Gabriella Sghia-Hughes, Kevin G Haworth, Ann E Woolfrey, Lauri M Burroughs, Grace Y Choi, Pamela S Becker, Hans-Peter Kiem