A comparison of intrauterine hemopoietic cell transplantation and lentiviral gene transfer for the correction of severe β-thalassemia in a HbbTh3/+ murine model
在HbbTh3/+小鼠模型中,比较宫内造血细胞移植和慢病毒基因转移治疗重型β-地中海贫血的效果
期刊:Experimental Hematology
影响因子:2.1
doi:10.1016/j.exphem.2018.03.006
Dighe, Niraja M; Tan, Kang Wei; Tan, Lay Geok; Shaw, Steven S W; Buckley, Suzanne M K; Sandikin, Dedy; Johana, Nuryanti; Tan, Yi-Wan; Biswas, Arijit; Choolani, Mahesh; Waddington, Simon N; Antoniou, Michael N; Chan, Jerry K Y; Mattar, Citra N Z