日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Splice-Modulating Antisense Oligonucleotides as Therapeutics for Inherited Metabolic Diseases

剪接调节反义寡核苷酸作为遗传代谢疾病的治疗药物

Chen, Suxiang; Heendeniya, Saumya Nishanga; Le, Bao T; Rahimizadeh, Kamal; Rabiee, Navid; Zahra, Qurat Ul Ain; Veedu, Rakesh N

Rational Design of Chimeric Antisense Oligonucleotides on a Mixed PO-PS Backbone for Splice-Switching Applications

基于混合PO-PS骨架的嵌合反义寡核苷酸的合理设计及其在剪接转换应用中的应用

Le, Bao T; Chen, Suxiang; Veedu, Rakesh N

Evaluation of Chemically Modified Nucleic Acid Analogues for Splice Switching Application

化学修饰核酸类似物在剪接转换应用中的评价

Le, Bao T; Chen, Suxiang; Veedu, Rakesh N

Genetic ablation of Pim1 or pharmacologic inhibition with TP-3654 ameliorates myelofibrosis in murine models

在小鼠模型中,Pim1基因敲除或使用TP-3654进行药理学抑制可改善骨髓纤维化。

Dutta, Avik; Nath, Dipmoy; Yang, Yue; Le, Bao T; Rahman, Mohammad Ferdous-Ur; Faughnan, Patrick; Wang, Zhenjia; Stuver, Matthew; He, Rongquan; Tan, Wuwei; Hutchison, Robert E; Foulks, Jason M; Warner, Steven L; Zang, Chongzhi; Mohi, Golam

Thiomorpholino oligonucleotides as a robust class of next generation platforms for alternate mRNA splicing

硫代吗啉代寡核苷酸作为一类强大的下一代mRNA选择性剪接平台

Le, Bao T; Paul, Sibasish; Jastrzebska, Katarzyna; Langer, Heera; Caruthers, Marvin H; Veedu, Rakesh N

Evaluation of DNA segments in 2'-modified RNA sequences in designing efficient splice switching antisense oligonucleotides

在设计高效剪接转换反义寡核苷酸时,评估2'端修饰的RNA序列中的DNA片段

Le, Bao T; Agarwal, Sudhir; Veedu, Rakesh N

Novel Disulfide-Bridged Bioresponsive Antisense Oligonucleotide Induces Efficient Splice Modulation in Muscle Myotubes in Vitro

新型二硫键桥联生物响应性反义寡核苷酸在体外诱导肌肉肌管细胞高效剪接调控

Le, Bao T; Kosbar, Tamer R; Veedu, Rakesh N

Antisense Oligonucleotides Targeting Angiogenic Factors as Potential Cancer Therapeutics

靶向血管生成因子的反义寡核苷酸作为潜在的癌症治疗药物

Le, Bao T; Raguraman, Prithi; Kosbar, Tamer R; Fletcher, Susan; Wilton, Steve D; Veedu, Rakesh N

Systematic evaluation of 2'-Fluoro modified chimeric antisense oligonucleotide-mediated exon skipping in vitro.

对 2'-氟修饰嵌合反义寡核苷酸介导的体外外显子跳跃进行系统评价

Chen Suxiang, Le Bao T, Chakravarthy Madhuri, Kosbar Tamer R, Veedu Rakesh N

Unlocked nucleic acid modified primer-based enzymatic polymerization assay: towards allele-specific genotype detection of human platelet antigens

解锁核酸修饰引物基酶促聚合测定法:用于人血小板抗原的等位基因特异性基因型检测

Le, Bao T; Hughes, Quintin; Rakesh, Shilpa; Baker, Ross; Jørgensen, Per T; Wengel, Jesper; Veedu, Rakesh N