日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Neuron-targeted gene therapy rescues multiple phenotypes of STXBP1-related disorders in mice and is well tolerated in nonhuman primates.

针对神经元的基因疗法可以挽救小鼠中多种 STXBP1 相关疾病的表型,并且在非人灵长类动物中具有良好的耐受性

Aeran Rangoli, Tanenhaus Annie, Sears Sheila M S, Moerke Nathan J, Miller Adam, Artur Camille, Bouhlal Yosr, Bove Peter F, Diaz de Arce Alexander J, Shimizu Saki, Le Jason, Place Keith, Hoffelt Dixon, Amarlkhagva Tselmeg, Su Jennifer, Chen Ming, Babineau Brooke A, McLaughlin John, Soe Myat, Macdonald Warren, Lin I Winnie, Bole Dhruv, Valentine Kristen M, Hallam Elizabeth, Dhanota Puja, Liu Serena, Tan Steven A, Zhao Ben, Hosur Raghavendra, Vila Maria Candida, Poda Suresh, Belle Archana, Tagliatela Stephanie

Collaborating With Schools for Public Health Research in England: Lessons Learned for Successful Partnerships

与英国学校合作开展公共卫生研究:成功合作的经验教训

Tsocheva, Ivelina; Chavda, Jasmine; Scales, James; Dove, Rosamund; Kalsi, Harpal; Wood, Helen E; Colligan, Grainne; Cross, Louise; Sartori, Luke; Moon, Jessica; Murray, Aisling; Van Den Berg, Sarah; Hirst, Alice; Mitchell, Jessica; Le, Jason; Balkwill, Frances; Petrovic, Kristian; Lie, Esther; Keating, Mia; Vincent Paul Raj, Britzer; Kotala, Pavani; Randhawa, Gurch; Mudway, Ian S; Griffiths, Chris

A living organoid biobank of patients with Crohn's disease reveals molecular subtypes for personalized therapeutics

克罗恩病患者的活体类器官生物样本库揭示了分子亚型,可用于个性化治疗

Courtney Tindle ,Ayden G Fonseca ,Sahar Taheri ,Gajanan D Katkar ,Jasper Lee ,Priti Maity ,Ibrahim M Sayed ,Stella-Rita Ibeawuchi ,Eleadah Vidales ,Rama F Pranadinata ,Mackenzie Fuller ,Dominik L Stec ,Mahitha Shree Anandachar ,Kevin Perry ,Helen N Le ,Jason Ear ,Brigid S Boland ,William J Sandborn ,Debashis Sahoo ,Soumita Das ,Pradipta Ghosh

VentX promotes tumor specific immunity and efficacy of immune checkpoint inhibitors

VentX可促进肿瘤特异性免疫和免疫检查点抑制剂的疗效。

Yi Le ,Hong Gao ,Joanna Le ,Jason L Hornick ,Ronald Bleday ,Jon Wee ,Zhenglun Zhu

The role of P2Y12 in the kinetics of microglial self-renewal and maturation in the adult visual cortex in vivo

P2Y12 在成人视觉皮层小胶质细胞自我更新和成熟动力学中的作用

Monique S Mendes, Linh Le, Jason Atlas, Zachary Brehm, Antonio Ladron-de-Guevara, Evelyn Matei, Cassandra Lamantia, Matthew N McCall, Ania K Majewska

Prion protein lowering is a disease-modifying therapy across prion disease stages, strains and endpoints

降低朊病毒蛋白水平是一种能够改善朊病毒疾病各个阶段、毒株和终点的疾病治疗手段。

Minikel, Eric Vallabh; Zhao, Hien T; Le, Jason; O'Moore, Jill; Pitstick, Rose; Graffam, Samantha; Carlson, George A; Kavanaugh, Michael P; Kriz, Jasna; Kim, Jae Beom; Ma, Jiyan; Wille, Holger; Aiken, Judd; McKenzie, Deborah; Doh-Ura, Katsumi; Beck, Matthew; O'Keefe, Rhonda; Stathopoulos, Jacquelyn; Caron, Tyler; Schreiber, Stuart L; Carroll, Jeffrey B; Kordasiewicz, Holly B; Cabin, Deborah E; Vallabh, Sonia M

Co-targeting of convergent nucleotide biosynthetic pathways for leukemia eradication

共同靶向聚合核苷酸生物合成途径以根除白血病

David A Nathanson, Amanda L Armijo, Michelle Tom, Zheng Li, Elizabeth Dimitrova, Wayne R Austin, Julian Nomme, Dean O Campbell, Lisa Ta, Thuc M Le, Jason T Lee, Ryan Darvish, Ari Gordin, Liu Wei, Hsiang-I Liao, Moses Wilks, Colette Martin, Saman Sadeghi, Jennifer M Murphy, Nidal Boulos, Michael E Ph

Activation of brainstem neurons by underwater diving in the rat

大鼠水下潜水激活脑干神经元

Panneton, W Michael; Gan, Qi; Le, Jason; Livergood, Robert S; Clerc, Philip; Juric, Rajko