Validation of a quantitative cell-based relative potency assay for LUXTURNA.
验证基于细胞的定量相对效力测定法对 LUXTURNA 的有效性
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2025.101423
High Katherine A, Le Blond Dave, Doucette Karen, Liu Dezhong, Farjo Rafal, Ignatova Irena, Buchlis George, Chung Daniel, Couto Linda B