日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Photoaffinity Ligand of Cystic Fibrosis Corrector VX-445 Identifies SCCPDH as an Off-Target.

囊性纤维化矫正剂 VX-445 的光亲和配体鉴定出 SCCPDH 为脱靶靶点

Kim Minsoo, Kim Kwangho, Lee Jesun, Barny Lea A, Scaggs Toya D, Romaine Ian M, Jeon KyuOk, Codreanu Simona G, Sherrod Stacy D, McLean John A, Naren Anjaparavanda P, Sulikowski Gary A, Plate Lars

Differential Expression and Microsystem Physiology Reveal Predominant and Drug Reversible CFTR-Related Defects in Idiopathic Pancreatitis

差异表达和微系统生理学揭示特发性胰腺炎中主要的、药物可逆的CFTR相关缺陷

Edisuriya, Paba; Liyanage, Pramodha; Lee, Jesun; Shetty, Anusha Jayesh; Liu, Hongyu; Tatonetti, Nicholas; Hutchings, Danielle; Freeman, Alvin J; Nathan, Jaimie D; Appakalai, Balamurugan; Pandol, Stephen J; Jegga, Anil G; Naren, Anjaparavanda P; Arora, Kavisha

A personalized medicine approach to optimize care for a pediatric cystic fibrosis patient with atypical clinical symptoms

采用个性化医疗方法优化对一名具有非典型临床症状的儿童囊性纤维化患者的治疗

Lee, Jesun; Husami, Ammar; Arora, Kavisha; Zhang, Weiqiang; Kadri, Ferdous; Yarlagadda, Sunitha; Moon, Changsuk; Mun, Kyu Shik; Zhang, Kejian; Huang, Yunjie; Liyanage, Pramodha; Brewington, John; Clancy, John P; Shaikhkhalil, Ala; Paul, Grace; Naren, Anjaparavanda P

Elexacaftor/Tezacaftor/Ivacaftor Improved Clinical Outcomes in a Patient with N1303K-CFTR Based on In Vitro Experimental Evidence

基于体外实验证据,Elexacaftor/Tezacaftor/Ivacaftor 可改善 N1303K-CFTR 患者的临床结局

Huang, Yunjie; Paul, Grace; Lee, Jesun; Yarlagadda, Sunitha; McCoy, Karen; Naren, Anjaparavanda P