日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Pridopidine in early-stage manifest Huntington's disease: a phase 3 trial

普利多吡啶治疗早期显性亨廷顿病:一项3期临床试验

Reilmann, Ralf; Feigin, Andrew; Rosser, Anne E; Kostyk, Sandra K; Saft, Carsten; Cohen, Yael; Schuring, Henk; Hand, Randal; Tan, Andrew M; Chen, Kelly; Feng, Wei; Navon-Perry, Leehee; Cruz-Herranz, Andres; Syltevik, Christine; Boot, Diderik; Squitieri, Ferdinando; Kayson, Elise; Mehra, Munish; Goldberg, Y Paul; Geva, Michal; Hayden, Michael R

The Safety Profile of Pridopidine, a Novel Sigma-1 Receptor Agonist for the Treatment of Huntington's Disease

普利多吡啶(一种用于治疗亨廷顿病的新型Sigma-1受体激动剂)的安全性概况

Goldberg, Yigal Paul; Navon-Perry, Leehee; Cruz-Herranz, Andrés; Chen, Kelly; Hecker-Barth, Gabriele; Spiegel, Katrin; Cohen, Yael; Niethammer, Martin; Tan, Andrew M; Schuring, Henk; Geva, Michal; Hayden, Michael R

HER2 and HLA-A*02 dual CAR-T cells utilize LOH in a NOT logic gate to address on-target off-tumor toxicity

HER2 和 HLA-A*02 双 CAR-T 细胞利用 NOT 逻辑门中的 LOH 来解决靶向肿瘤外毒性

David Bassan #, Leehee Weinberger #, Jason Yi #, Tanya Kim, Michael R Weist, Gregor B Adams, Orit Foord, Neta Chaim, Sarit Tabak, Nir Bujanover, Yael Lopesco, Kristina Vucci, Caitlin Schnair, Limor Levy-Knafo, Richard L Kendall, Frank J Calzone, Adi Sharbi-Yunger

Principles of signaling pathway modulation for enhancing human naive pluripotency induction

信号通路调节增强人类幼稚多能性诱导的原理

Jonathan Bayerl, Muneef Ayyash, Tom Shani, Yair Shlomo Manor, Ohad Gafni, Rada Massarwa, Yael Kalma, Alejandro Aguilera-Castrejon, Mirie Zerbib, Hadar Amir, Daoud Sheban, Shay Geula, Nofar Mor, Leehee Weinberger, Segev Naveh Tassa, Vladislav Krupalnik, Bernardo Oldak, Nir Livnat, Shadi Tarazi, Shadi

Deterministic Somatic Cell Reprogramming Involves Continuous Transcriptional Changes Governed by Myc and Epigenetic-Driven Modules

确定性体细胞重编程涉及由 Myc 和表观遗传驱动模块控制的连续转录变化

Asaf Zviran, Nofar Mor, Yoach Rais, Hila Gingold, Shani Peles, Elad Chomsky, Sergey Viukov, Jason D Buenrostro, Roberta Scognamiglio, Leehee Weinberger, Yair S Manor, Vladislav Krupalnik, Mirie Zerbib, Hadas Hezroni, Diego Adhemar Jaitin, David Larastiaso, Shlomit Gilad, Sima Benjamin, Ohad Gafni, A

Quantification of Motor Function in Huntington Disease Patients Using Wearable Sensor Devices

利用可穿戴传感器设备量化亨廷顿病患者的运动功能

Gordon, Mark Forrest; Grachev, Igor D; Mazeh, Itzik; Dolan, Yonatan; Reilmann, Ralf; Loupe, Pippa S; Fine, Shai; Navon-Perry, Leehee; Gross, Nicholas; Papapetropoulos, Spyros; Savola, Juha-Matti; Hayden, Michael R

Characterizing patient compliance over six months in remote digital trials of Parkinson's and Huntington disease

在帕金森病和亨廷顿病的远程数字试验中,对患者六个月的依从性进行表征

Cohen, Shani; Waks, Zeev; Elm, Jordan J; Gordon, Mark Forrest; Grachev, Igor D; Navon-Perry, Leehee; Fine, Shai; Grossman, Iris; Papapetropoulos, Spyros; Savola, Juha-Matti

SOX17 is a critical specifier of human primordial germ cell fate

SOX17是人类原始生殖细胞命运的关键决定因子。

Naoko Irie ,Leehee Weinberger ,Walfred W C Tang ,Toshihiro Kobayashi ,Sergey Viukov ,Yair S Manor ,Sabine Dietmann ,Jacob H Hanna ,M Azim Surani

Transient acquisition of pluripotency during somatic cell transdifferentiation with iPSC reprogramming factors

利用 iPSC 重编程因子在体细胞转分化过程中瞬时获得多能性

Itay Maza, Inbal Caspi, Asaf Zviran, Elad Chomsky, Yoach Rais, Sergey Viukov, Shay Geula, Jason D Buenrostro, Leehee Weinberger, Vladislav Krupalnik, Suhair Hanna, Mirie Zerbib, James R Dutton, William J Greenleaf, Rada Massarwa, Noa Novershtern, Jacob H Hanna

Monoubiquitinylation regulates endosomal localization of Lst2, a negative regulator of EGF receptor signaling

单泛素化调节 Lst2 的内体定位,Lst2 是 EGF 受体信号的负调节剂

Yaron Mosesson, David Chetrit, Leehee Schley, Janina Berghoff, Tamar Ziv, Silvia Carvalho, Fernanda Milanezi, Arie Admon, Fernando Schmitt, Marcelo Ehrlich, Yosef Yarden