Pridopidine in early-stage manifest Huntington's disease: a phase 3 trial
普利多吡啶治疗早期显性亨廷顿病:一项3期临床试验
期刊:Nature Medicine
影响因子:50
doi:10.1038/s41591-025-03920-3
Reilmann, Ralf; Feigin, Andrew; Rosser, Anne E; Kostyk, Sandra K; Saft, Carsten; Cohen, Yael; Schuring, Henk; Hand, Randal; Tan, Andrew M; Chen, Kelly; Feng, Wei; Navon-Perry, Leehee; Cruz-Herranz, Andres; Syltevik, Christine; Boot, Diderik; Squitieri, Ferdinando; Kayson, Elise; Mehra, Munish; Goldberg, Y Paul; Geva, Michal; Hayden, Michael R