日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

NLRP3 inflammasome blockade treats intestinal inflammation associated with chronic granulomatous disease

NLRP3炎症小体阻断可治疗与慢性肉芽肿病相关的肠道炎症

Darbinian, Emma; Mlaga, Kodjovi D; Aranguren, Matheus; Desjardins, Aléhandra; Martineau, Evelyne; Massé, Chantal; Leiding, Jennifer W; Poudrier, Johanne; Falcone, Emilia Liana

Outcomes following matched sibling donor transplantation for severe combined immunodeficiency: a report from the PIDTC

同胞相合供体移植治疗重症联合免疫缺陷的疗效:来自PIDTC的报告

Rayes, Ahmad; Logan, Brent R; Liu, Xuerong; Dara, Jasmeen; Buckley, Rebecca H; Oved, Joseph H; Kapoor, Neena; Kapadia, Malika; Chandra, Sharat; Martinez, Caridad A; Bunin, Nancy J; Chandrakasan, Shanmuganathan; Chen, Karin; Bednarski, Jeffrey J; Haines, Hilary L; Eissa, Hesham; Talano, Julie-An M; Keller, Michael D; Ebens, Christen L; Chaudhury, Sonali; Shereck, Evan B; Aquino, Victor M; Knutsen, Alan P; Alexander, Jessie L; Gillio, Alfred P; Chellapandian, Deepakbabu; Shah, Ami J; Miller, Holly K; Vander Lugt, Mark T; Seroogy, Christine M; Dorsey, Morna J; Mousallem, Talal; Parrott, Roberta E; O'Reilly, Richard J; Aguayo-Hiraldo, Paibel I; Prockop, Susan E; Dávila Saldaña, Blachy J; Thakar, Monica S; Burroughs, Lauri M; Torgerson, Troy R; Leiding, Jennifer W; Marsh, Rebecca A; Griffith, Linda M; Pulsipher, Michael A; Kohn, Donald B; Notarangelo, Luigi; Cowan, Morton J; Puck, Jennifer M; Cuvelier, Geoffrey D E; Heimall, Jennifer; Haddad, Elie; Pai, Sung-Yun; Dvorak, Christopher C

Emapalumab use in malignancy-associated hemophagocytic lymphohistiocytosis in the United States: the REAL-HLH study

美国恶性肿瘤相关噬血细胞性淋巴组织细胞增生症中使用依帕利单抗:REAL-HLH 研究

Zoref-Lorenz, Adi; Allen, Carl E; Behrens, Edward M; Chandrakasan, Shanmuganathan; Chien, May; Hermiston, Michelle L; Hinson, Ashley P; Intzes, Stefanos; Isakoff, Michael S; Leiding, Jennifer W; Oladapo, Abiola; Panigrahi, Arun; Patel, Sachit A; Pednekar, Priti; Ray, Anish K; Rothman, Jennifer A; Saldaña, Blachy Dávila; Walkovich, Kelly J; Weinstein, Joanna; Yee, John D; Jordan, Michael B; Weinstein, Joanna; Hinson, Ashley P; Allen, Carl E; Eckstein, Olive S; Gulati, Nitya; Chandrakasan, Shanmuganathan; Haines, Hilary; Nakano, Taizo A; Patel, Sachit A; Behrens, Edward M; Intzes, Stefanos; Hays, Allyson; Saldaña, Blachy Dávila; Jordan, Michael B; Zoref-Lorenz, Adi; Hanna, Rabi; Isakoff, Michael; Ray, Anish K; Rothman, Jennifer A; Tandra, Anand; Cooper, Robert; Leiding, Jennifer W; Chien, May; Sarangi, Susmita; Gidvani-Diaz, Vinod K; Satwani, Prakash; Carter, John; Henry, Michael; Gloude, Nicholas; Bhatt, Sima; Bhatla, Deepika; Draper, Lauren; Panigrahi, Arun; Hermiston, Michelle L; Modica, Renee; Riskalla, Mona; Baker, Ashley; Ward, Brant

Hematopoietic cell transplantation for Wiskott-Aldrich syndrome: a PIDTC report

造血干细胞移植治疗威斯科特-奥尔德里奇综合征:PIDTC报告

Alexander, Jessie L; Dávila Saldaña, Blachy J; Brazauskas, Ruta; Dammalapati, Sravya Gethika; Griffith, Linda M; Shah, Ami J; Shimano, Kristin A; Ochs, Hans D; Bleesing, Jack J; Ebens, Christen L; Kapadia, Malika; Bauchat, Andrea; Kapoor, Neena; Oved, Joseph H; Eissa, Hesham; Lust, Hannah; Keller, Michael D; Haines, Hilary; Chandrakasan, Shanmuganathan; Talano, Julie-An; Rayes, Ahmad; Madden, Lisa; Shereck, Evan; Miller, Holly K; Satter, Lisa Forbes; Martinez, Caridad; Rozmus, Jacob; Bednarski, Jeffrey J; Yu, Lolie C; Chellapandian, Deepakbabu; Aquino, Victor M; Knutsen, Alan; Chong, Hey; Chopek, Ashley; Gillio, Alfred P; Joshi, Avni; Rangarajan, Hemalatha; Moore, Theodore B; Andolina, Jeffrey R; DeSantes, Kenneth B; Vander Lugt, Mark; Prockop, Susan E; Shyr, David C; Sullivan, Kathleen E; Parikh, Suhag; Weinacht, Katja G; Torgerson, Troy R; Marsh, Rebecca; Dvorak, Christopher C; Chan, Alice Y; Haddad, Elie; Heimall, Jennifer R; Pulsipher, Michael A; Leiding, Jennifer W; Kohn, Donald B; Puck, Jennifer M; Notarangelo, Luigi D; Rawlings, David J; Cowan, Morton J; Petrovic, Aleksandra; Pai, Sung-Yun; Burroughs, Lauri M

Umbilical Cord Blood Transplantation Provides an Alternative for Patients With Chronic Granulomatous Disease Lacking HLA-Matched Donors: A PIDTC Report

脐带血移植为缺乏HLA匹配供体的慢性肉芽肿病患者提供了一种替代方案:PIDTC报告

Arnold, Danielle E; Leiding, Jennifer W; Logan, Brent; Marsh, Rebecca A; Griffith, Linda M; Grunebaum, Eyal; Murguía-Favela, Luis; Mallhi, Kanwaldeep; Chellapandian, Deepakbabu; Deal, Christin L; Lim, Stephanie Si; Prasad, Vinod; Heimall, Jennifer; Chandrakasan, Shanmuganathan; Chen, Karin; Yu, Lolie C; Seroogy, Christine M; Gillio, Alfred; Bednarski, Jeffrey J; Kapoor, Neena; Moore, Theodore B; Cuvelier, Geoffrey D E; Touzot, Fabien; Rayes, Ahmad; Ebens, Christen L; Schaefer, Edo; Bauchat, Andrea; Chopek, Ashley; Burroughs, Lauri; Cowan, Morton J; Dvorak, Christopher C; Haddad, Elie; Kohn, Donald B; Notarangelo, Luigi D; Pai, Sung-Yun; Puck, Jennifer M; Pulsipher, Michael A; Torgerson, Troy; Malech, Harry L; Kang, Elizabeth M; Parikh, Suhag

Clinical spectrum of Wiskott-Aldrich syndrome carriers: Self-reported survey of 193 carriers

Wiskott-Aldrich综合征携带者的临床表现谱:193名携带者的自我报告调查

Chandrakasan, Shanmuganathan; Westbrook, Adrianna; Griffith, Linda M; Hagin, David; Iyengar, Sumathi; Mangurian, Christina; Scalchunes, Chris; Sullivan, Kathleen E; Zablocki, Akiva; Bakshi, Nitya; Sinha, Cynthia; Burroughs, Lauri M; Chan, Alice Y; Dvorak, Christopher C; Haddad, Elie; Heimall, Jennifer; Kohn, Donald B; Leiding, Jennifer W; Notarangelo, Luigi D; Pai, Sung-Yun; Puck, Jennifer M; Pulsipher, Michael A; Marsh, Rebecca A; Torgerson, Troy; Cowan, Morton J; Ochs, Hans D; Parikh, Suhag

Neurodevelopmental outcomes following hematopoietic cell transplantation for patients with severe combined immunodeficiency (SCID): A PIDTC study

造血干细胞移植治疗重症联合免疫缺陷(SCID)患者的神经发育结局:一项PIDTC研究

Brumm, Virdette L; Kidd, Sharon A; Logan, Brent R; Chunara, Farheen; Heimall, Jennifer; Griffith, Linda M; Kohn, Donald B; Sanchez, Lauren; Bednarski, Jeffrey J; Martinez, Caridad; Lugt, Mark Vander; Kapoor, Neena; Wright, Nicola; Spitzer, Barbara; Oved, Joseph H; Chandra, Sharat; Chellapandian, Deepak; Ebens, Christen L; Petrovic, Aleks; Rayes, Ahmad; Haines, Hilary L; Lust, Hannah; Schofield, Hannah-Lise Tirado; Christopher, Lauren; Harris, Lynnette L; Satter, Lisa Forbes; Burroughs, Lauri; Dvorak, Christopher C; Haddad, Elie; Leiding, Jennifer W; Marsh, Rebecca A; Notarangelo, Luigi D; Pai, Sung Yun; Pulsipher, Michael A; Puck, Jennifer M; Cowan, Morton J; Shah, Ami J

International clinical consensus on leukocyte adhesion deficiency-I: Modified Delphi analysis

关于白细胞黏附缺陷的国际临床共识-I:改良德尔菲分析

Heimall, Jennifer; González-Granado, Luis Ignacio; Booth, Claire; Ip, Winnie; Kuo, Caroline Y; Bakhtiar, Shahrzad; Ikincioğullari, Aydan; Ferrua, Francesca; Chitty-Lopez, Maria; Bailey, Miranda; Carter, Patrice; Matthews, Emily; Lee, Jennifer; Prockop, Susan; Gennery, Andrew R; Leiding, Jennifer W

Multiomics dissection of human RAG deficiency reveals distinctive patterns of immune dysregulation but a common inflammatory signature.

对人类 RAG 缺陷的多组学分析揭示了独特的免疫失调模式,但具有共同的炎症特征。

Bosticardo Marita, Dobbs Kerry, Delmonte Ottavia M, Martins Andrew J, Pala Francesca, Kawai Tomoki, Kenney Heather, Magro Gloria, Rosen Lindsey B, Yamazaki Yasuhiro, Yu Hsin-Hui, Calzoni Enrica, Lee Yu Nee, Liu Can, Stoddard Jennifer, Niemela Julie, Fink Danielle, Castagnoli Riccardo, Ramba Meredith, Cheng Aristine, Riley Deanna, Oikonomou Vasileios, Shaw Elana, Belaid Brahim, Keles Sevgi, Al-Herz Waleed, Cancrini Caterina, Cifaldi Cristina, Baris Safa, Sharapova Svetlana, Schuetz Catharina, Gennery Andrew R, Freeman Alexandra F, Somech Raz, Choo Sharon, Giliani Silvia C, Güngör Tayfun, Drozdov Daniel, Meyts Isabelle, Moshous Despina, Neven Benedicte, Abraham Roshini S, El-Marsafy Aisha, Kanariou Maria, King Alejandra, Licciardi Francesco, Cruz-Muñoz Mario E, Palma Paolo, Poli Cecilia, Adeli Mehdi, Algeri Mattia, Alroqi Fayhan J, Bastard Paul, Bergerson Jenna R E, Booth Claire, Brett Ana, Burns Siobhan O, Butte Manish J, Padem Nurcicek, de la Morena M, Dbaibo Ghassan, de Ravin Suk See, Dimitrova Dimana, Djidjik Reda, Dorna Mayra B, Dutmer Cullen M, Elfeky Reem, Facchetti Fabio, Fuleihan Ramsay L, Geha Raif S, Gonzalez-Granado Luis I, Haljasmägi Liis, Ale Hanadys, Hayward Anthony, Hifanova Anna M, Ip Winnie, Kaplan Blanka, Kapoor Neena, Karakoc-Aydiner Elif, Kärner Jaanika, Keller Michael D, Dávila Saldaña Blachy J, Kiykim Ayça, Kuijpers Taco W, Kuznetsova Elena E, Latysheva Elena A, Leiding Jennifer W, Locatelli Franco, Alva-Lozada Guisela, McCusker Christine, Celmeli Fatih, Morsheimer Megan, Ozen Ahmet, Parvaneh Nima, Pasic Srdjan, Plebani Alessandro, Preece Kahn, Prockop Susan, Sakovich Inga S, Starkova Elena E, Torgerson Troy, Verbsky James, Walter Jolan E, Ward Brant, Wisner Elizabeth L, Draper Deborah, Myint-Hpu Katherine, Truong Pooi M, Lionakis Michail S, Similuk Morgan B, Walkiewicz Magdalena A, Klion Amy, Holland Steven M, Oguz Cihan, Bogunovic Dusan, Kisand Kai, Su Helen C, Tsang John S, Kuhns Douglas, Villa Anna, Rosenzweig Sergio D, Pittaluga Stefania, Notarangelo Luigi D

Inborn errors of immunity reveal molecular requirements for generation and maintenance of human CD4(+) IL-9-expressing cells

先天性免疫缺陷揭示了人类CD4(+)IL-9表达细胞生成和维持的分子需求

Rao, Geetha; Mack, Corinne D; Nguyen, Tina; Wong, Natalie; Payne, Kathryn; Worley, Lisa; Gray, Paul E; Wong, Melanie; Hsu, Peter; Stormon, Michael O; Preece, Kahn; Suan, Daniel; O'Sullivan, Michael; Blincoe, Annaliesse K; Sinclair, Jan; Okada, Satoshi; Hambleton, Sophie; Arkwright, Peter D; Boztug, Kaan; Stepensky, Polina; Cooper, Megan A; Bezrodnik, Liliana; Nadeau, Kari C; Abolhassani, Hassan; Abraham, Roshini S; Seppänen, Mikko R J; Béziat, Vivien; Bustamante, Jacinta; Forbes Satter, Lisa R; Leiding, Jennifer W; Meyts, Isabelle; Jouanguy, Emmanuelle; Boisson-Dupuis, Stéphanie; Uzel, Gulbu; Puel, Anne; Casanova, Jean-Laurent; Tangye, Stuart G; Ma, Cindy S