Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1
SCID-X1逆转录病毒介导的基因治疗后4例患者发生插入性肿瘤发生
期刊:Journal of Clinical Investigation
影响因子:13.3
doi:10.1172/JCI35700.
Salima Hacein-Bey-Abina,Alexandrine Garrigue, Gary P Wang, Jean Soulier, Annick Lim, Estelle Morillon, Emmanuelle Clappier, Laure Caccavelli, Eric Delabesse, Kheira Beldjord, Vahid Asnafi, Elizabeth MacIntyre, Liliane Dal Cortivo, Isabelle Radford, Nicole Brousse, François Sigaux, Despina Moshous, Julia Hauer, Arndt Borkhardt, Bernd H Belohradsky, Uwe Wintergerst, Maria C Velez, Lily Leiva, Ricardo Sorensen, Nicolas Wulffraat, Stéphane Blanche, Frederic D Bushman, Alain Fischer, Marina Cavazzana-Calvo