Etranacogene dezaparvovec in people with hemophilia B and without adeno-associated virus serotype 5 neutralizing antibodies: a 4-year subgroup analysis of the Health Outcomes with Padua Gene; Evaluation in Hemophilia B (HOPE-B) trial
在不具有腺相关病毒5型中和抗体的B型血友病患者中应用依曲那康基因治疗:一项为期4年的帕多瓦基因治疗B型血友病健康结局评估(HOPE-B)试验亚组分析
期刊:Research and Practice in Thrombosis and Haemostasis
影响因子:3.4
doi:10.1016/j.rpth.2025.103321
Raheja, Priyanka; O'Connell, Niamh; Verhamme, Peter; Kampmann, Peter; Lemons, Richard S; Wang, Fei; Gill, Sean; Monahan, Paul E; Le Quellec, Sandra; Leebeek, Frank W G