Differences in swallowing efficacy of disease modifying treatment between infants receiving pre-symptomatic and symptomatic administration
接受疾病改善治疗的婴儿在症状前和症状后给药方面,吞咽疗效存在差异
期刊:Orphanet Journal of Rare Diseases
影响因子:3.5
doi:10.1186/s13023-025-04049-9
McGrattan, Katlyn Elizabeth; Mohr, Alicia Hofelich; Miles, Anna; Allen, Jacqui; Ochura, Juliet; Hernandez, Kayla; Walsh, Katie; Rao, Vamshi; Stevens, Melanie; McGhee, Heather; Nichols, Keeley; Turksi, Morgan Elaine; Spoden, Abigail; Wilson, Irena; Coker, Mackenzi; Leon-Astudillo, Carmen; Smith, Leann Schow; Brandsema, John; Farah, Hiba; Welc, Julia; Levy, Deborah; Clements, Miranda; Duong, Tina; Young, Sally Dunaway; Schenck, Graham; Richardson, Randal; Karachunski, Peter; Brown, Ashley; Brown, Allison; Castro, Diana; Darras, Basil T; Graham, Robert J