Perm1 Gene Therapy Mitigates PRDM16-Associated Cardiomyopathy
Perm1基因疗法可减轻PRDM16相关性心肌病
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doi:10.64898/2026.04.13.718330
Rouzbehani, Omid Mt; Stephens, Sophie; Werbner, Ben; Szulik, Marta W; Sun, Bo; Hua, Mira; Watanabe, Shinya; Leonelli, Ava; Goodman, Michael; Bia, Ryan; Davey, Crystal F; Golkowski, Martin G; Franklin, Sarah; Landstrom, Andrew P; Boudina, Sihem