日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Early life safety profiling of gene therapy for spinal muscular atrophy

脊髓性肌萎缩症基因疗法的早期生命安全性评估

Spellman, Rebecca G; Ha, Leillani L; Da Silva Duarte Lepez, Salomé; Arruda, Elizabeth A; Rodrigues, Emma; Swoboda, Kathryn J; Alves, Christiano R R

Cardiac defects in spinal muscular atrophy and the role of SMN in cardiomyocyte homeostasis

脊髓性肌萎缩症的心脏缺陷及SMN在心肌细胞稳态中的作用

Garner, Reid; Ha, Leillani L; Nery, Flavia C; Spellman, Rebecca G; Chehade, Lucia; Eichelberger, Eric J; Da Silva Duarte Lepez, Salomé; Johnstone, Alec J; Kothary, Rashmi; Swoboda, Kathryn J; Alves, Christiano R R

In situ endoscopic photodynamic therapy combined with immature DC vaccination induces a robust T cell response against peritoneal carcinomatosis

原位内镜光动力疗法联合未成熟树突状细胞疫苗接种可诱导针对腹膜癌的强效T细胞反应。

Charline Degavre ,Anouk Lepez ,Sebastien Ibanez ,Clémence François ,Katarzyna Głowacka ,Céline Guilbaud ,Florine Laloux-Morris ,Hrag Esfahani ,Davide Brusa ,Caroline Bouzin ,Olivier Feron

A novel mitochondrial pyruvate carrier inhibitor drives stem cell-like memory CAR T cell generation and enhances antitumor efficacy

新型线粒体丙酮酸载体抑制剂可驱动类干细胞记忆 CAR-T 细胞生成并增强抗肿瘤功效

Mathias Wenes, Anouk Lepez, Vladimir Arinkin, Kinsey Maundrell, Orsolya Barabas, Federico Simonetta, Valérie Dutoit, Pedro Romero, Jean-Claude Martinou, Denis Migliorini

The mitochondrial pyruvate carrier regulates memory T cell differentiation and antitumor function

线粒体丙酮酸载体调节记忆性T细胞分化和抗肿瘤功能

Mathias Wenes ,Alison Jaccard ,Tania Wyss ,Noelia Maldonado-Pérez ,Shao Thing Teoh ,Anouk Lepez ,Fabrice Renaud ,Fabien Franco ,Patrice Waridel ,Céline Yacoub Maroun ,Benjamin Tschumi ,Nina Dumauthioz ,Lianjun Zhang ,Alena Donda ,Francisco Martín ,Denis Migliorini ,Sophia Y Lunt ,Ping-Chih Ho ,Pedro Romero

Whole-blood dysregulation of actin-cytoskeleton pathway in adult spinal muscular atrophy patients

成年脊髓性肌萎缩症患者全血肌动蛋白细胞骨架通路失调

Jennifer J Siranosian, Flavia C Nery, Christiano R R Alves, Benjamin A Siranosian, Nicholas J Lyons, Eric J Eichelberger, Reid Garner, Salomé Da Silva Duarte Lepez, Alec J Johnstone, Aravind Subramanian, Kathryn J Swoboda

Long-term T cell fitness and proliferation is driven by AMPK-dependent regulation of reactive oxygen species

长期 T 细胞适应性和增殖是由 AMPK 依赖的活性氧调节驱动的

Anouk Lepez, Tiphène Pirnay, Sébastien Denanglaire, David Perez-Morga, Marjorie Vermeersch, Oberdan Leo, Fabienne Andris

CRISPR/Cas9 mediated knockout of rb1 and rbl1 leads to rapid and penetrant retinoblastoma development in Xenopus tropicalis

利用 CRISPR/Cas9 介导的 rb1 和 rbl1 基因敲除导致非洲爪蟾视网膜母细胞瘤的快速且高致病性发展

Naert, Thomas; Colpaert, Robin; Van Nieuwenhuysen, Tom; Dimitrakopoulou, Dionysia; Leoen, Jannick; Haustraete, Jurgen; Boel, Annekatrien; Steyaert, Wouter; Lepez, Trees; Deforce, Dieter; Willaert, Andy; Creytens, David; Vleminckx, Kris

Fetal microchimeric cells in autoimmune thyroid diseases: harmful, beneficial or innocent for the thyroid gland?

胎儿微嵌合细胞在自身免疫性甲状腺疾病中的作用:对甲状腺有害、有益还是无害?

Lepez, Trees; Vandewoestyne, Mado; Deforce, Dieter

Fetal microchimeric cells in blood of women with an autoimmune thyroid disease

患有自身免疫性甲状腺疾病的女性血液中的胎儿微嵌合细胞

Trees Lepez, Mado Vandewoestyne, Shahid Hussain, Filip Van Nieuwerburgh, Kris Poppe, Brigitte Velkeniers, Jean-Marc Kaufman, Dieter Deforce