日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Novel humanized loss-of-function NF1 mouse model of juvenile myelomonocytic leukemia.

新型人源化功能缺失型 NF1 小鼠幼年型骨髓单核细胞白血病模型。

Sinha Roshani, Patil Rachana Vinay, Romano Rosa, Sharma Devesh, Lee Esmond, Perriman Rhonda, Takeda Saori, Lesch Benjamin J, Yao Zhenyu, Liu Y Lucy, Cromer M Kyle, Porteus Matthew H, Bertaina Alice

Combinatorial base editing couples disease correction with lineage amplification in hematopoietic stem and progenitor cells

组合碱基编辑技术将疾病矫正与造血干细胞和祖细胞的谱系扩增相结合

Jia, Kun; Soupene, Eric; Sinha, Roshani; Lesch, Benjamin J; Pendergast, Michael A; Choi, Rachel; Zhang, Xinyi; Foppiani, Elisabetta M; Kostamo, Zachary; Chu, Simon N; Sharma, Devesh; Yu, Xinjie; Cordero, Marco; Walters, Mark C; MacKenzie, Tippi C; Sheehan, Vivien A; Cromer, M Kyle

Protocol for efficient CRISPR/AAV-mediated genome editing and erythroid differentiation of human hematopoietic stem and progenitor cells.

利用 CRISPR/AAV 介导的基因组编辑和人类造血干细胞及祖细胞红系分化的有效方案

Sharma Devesh, Sinha Roshani, Lesch Benjamin J, Cromer M Kyle

Discovery of a pre-vein progenitor that requires VEGF/ERK inhibition to complete vein differentiation.

发现一种前静脉祖细胞,需要抑制 VEGF/ERK 才能完成静脉分化。

Ang Lay Teng, Zheng Sherry Li, Liu Kevin J, Masaltseva Anastasiia, Winters June, von Creytz Isabel, Jha Sawan K, Yin Qingqing, Qian Crystal, Xiong Xiaochen, Dailamy Amir, Xi Ellie, Alcocer Juan C, Sorensen Daniel W, She Richard, Smolyar Karina, Szumska Dorota, Nornes Svanhild, Martin Renata M, Lesch Benjamin J, Restrepo Nicole K, Sun Wenfei, Weissman Jonathan S, Lickert Heiko, Porteus Matthew H, Skylar-Scott Mark A, Mosimann Christian, Sumanas Saulius, Val Sarah De, Prescott Joseph B, Red-Horse Kristy, Loh Kyle M

Combining Cell-Intrinsic and -Extrinsic Resistance to HIV-1 By Engineering Hematopoietic Stem Cells for CCR5 Knockout and B Cell Secretion of Therapeutic Antibodies

通过基因工程改造造血干细胞,使其CCR5基因敲除并分泌B细胞治疗性抗体,从而结合细胞内在和外在的抗HIV-1能力

Feist, William N; Luna, Sofia E; Ben-Efraim, Kaya; Filsinger Interrante, Maria V; Amorin, Nelson A; Johnston, Nicole M; Bruun, Theodora U J; Ghanim, Hana Y; Lesch, Benjamin J; Dudek, Amanda M; Porteus, Matthew H