日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Author Correction: In vivo base editing extends lifespan of a humanized mouse model of prion disease

作者更正:体内碱基编辑延长了朊病毒病人源化小鼠模型的寿命

An, Meirui; Davis, Jessie R; Levy, Jonathan M; Serack, Fiona E; Harvey, John W; Brauer, Pamela P; Pirtle, Catherine P; Berríos, Kiara N; Newby, Gregory A; Yeh, Wei-Hsi; Kamath, Nikita; Mortberg, Meredith; Lian, Yuan; Howard, Michael; DeSouza-Lenz, Kendrick; Guzman, Kenia; Thai, Aaron; Graffam, Samantha; Laversenne, Vanessa; Coffey, Alissa A; Frei, Jeannine; Pierce, Sarah E; Safar, Jiri G; Deverman, Benjamin E; Minikel, Eric Vallabh; Vallabh, Sonia M; Liu, David R

In vivo base editing extends lifespan of a humanized mouse model of prion disease.

体内碱基编辑延长了朊病毒疾病人源化小鼠模型的寿命

An Meirui, Davis Jessie R, Levy Jonathan M, Serack Fiona E, Harvey John W, Brauer Pamela P, Pirtle Catherine P, Berríos Kiara N, Newby Gregory A, Yeh Wei-Hsi, Kamath Nikita, Mortberg Meredith, Lian Yuan, Howard Michael, DeSouza-Lenz Kendrick, Guzman Kenia, Thai Aaron, Graffam Samantha, Laversenne Vanessa, Coffey Alissa A, Frei Jeannine, Pierce Sarah E, Safar Jiri G, Deverman Benjamin E, Minikel Eric Vallabh, Vallabh Sonia M, Liu David R

ODP326 Isolated Abducens Palsy as a Presenting Feature of Pituitary Apoplexy

ODP326 孤立性外展神经麻痹作为垂体卒中的首发症状

Davis, Jessie R; Wang, Xiao; Witte, Isaac P; Huang, Tony P; Levy, Jonathan M; Raguram, Aditya; Banskota, Samagya; Seidah, Nabil G; Musunuru, Kiran; Liu, David R; Lai, William; Naidoo, Shiva; Yossef, Kristena; Das, Niladri; Baidya, Arjun; Tarenia, Silima Subhasnigdha; Hathi, Deep; Gaikwad, Prashant Manohar; Pathak, Yashaswi; Banerjee, Abhirup; Chatterjee, Mounam; Goswami, Soumik; Sengupta, Nilanjan; Branis, Natalia; Thota, Geethika; Nezu, Masahiro; Satou, Motoyasu; Nakano-Tateno, Tae; Chik, Constance L; Tateno, Toru; Ren, Hongxia; Atila, Cihan; Christ-Crain, Mirjam; Gaisl, Odile; Szinnai, Gabor; Vogt, Deborah; Werlen, Laura; Cuenca, Dalia; Tovar-Mendez, Victor Hugo; Gómez-Pérez, Francisco; Toy, Brandon Altar-Trejo; Cuevas-Ramos, Daniel; Thota, Geethika; Raj, Kavin; Dewan, Sandesh; Alam, Mustafa; Alam, Mustafa; Abdelrahim, Baha; Alam, Mahad; Horani, Mohamed Hosam

In vivo base editing restores sensory transduction and transiently improves auditory function in a mouse model of recessive deafness

体内碱基编辑可恢复隐性耳聋小鼠模型的听觉转导并暂时改善听觉功能

Yeh, Wei-Hsi; Shubina-Oleinik, Olga; Levy, Jonathan M; Pan, Bifeng; Newby, Gregory A; Wornow, Michael; Burt, Rachel; Chen, Jonathan C; Holt, Jeffrey R; Liu, David R

Continuous evolution of base editors with expanded target compatibility and improved activity.

碱基编辑器不断发展,具有更广泛的靶标兼容性和更高的活性

Thuronyi B W, Koblan Luke W, Levy Jonathan M, Yeh Wei-Hsi, Zheng Christine, Newby Gregory A, Wilson Christopher, Bhaumik Mantu, Shubina-Oleinik Olga, Holt Jeffrey R, Liu David R

Improving cytidine and adenine base editors by expression optimization and ancestral reconstruction

通过表达优化和祖先序列重建改进胞嘧啶和腺嘌呤碱基编辑器

Koblan, Luke W; Doman, Jordan L; Wilson, Christopher; Levy, Jonathan M; Tay, Tristan; Newby, Gregory A; Maianti, Juan Pablo; Raguram, Aditya; Liu, David R

Increasing the genome-targeting scope and precision of base editing with engineered Cas9-cytidine deaminase fusions

利用工程化Cas9-胞嘧啶脱氨酶融合蛋白提高碱基编辑的基因组靶向范围和精确度

Kim, Y Bill; Komor, Alexis C; Levy, Jonathan M; Packer, Michael S; Zhao, Kevin T; Liu, David R

Subunit-specific role for the amino-terminal domain of AMPA receptors in synaptic targeting

AMPA受体氨基末端结构域在突触靶向中的亚基特异性作用

Díaz-Alonso, Javier; Sun, Yujiao J; Granger, Adam J; Levy, Jonathan M; Blankenship, Sabine M; Nicoll, Roger A

Membrane-associated guanylate kinase dynamics reveal regional and developmental specificity of synapse stability

膜相关鸟苷酸激酶的动态变化揭示了突触稳定性的区域性和发育特异性

Levy, Jonathan M; Nicoll, Roger A

Synaptic Consolidation Normalizes AMPAR Quantal Size following MAGUK Loss

MAGUK缺失后,突触巩固可使AMPA受体量子大小恢复正常

Levy, Jonathan M; Chen, Xiaobing; Reese, Thomas S; Nicoll, Roger A