In vivo genome editing in mouse restores dystrophin expression in Duchenne muscular dystrophy patient muscle fibers
小鼠体内基因组编辑恢复杜氏肌营养不良症患者肌纤维中的肌营养不良蛋白表达
期刊:Genome Medicine
影响因子:10.4
doi:10.1186/s13073-021-00876-0
Menglong Chen #, Hui Shi #, Shixue Gou #, Xiaomin Wang, Lei Li, Qin Jin, Han Wu, Huili Zhang, Yaqin Li, Liang Wang, Huan Li, Jinfu Lin, Wenjing Guo, Zhiwu Jiang, Xiaoyu Yang, Anding Xu, Yuling Zhu, Cheng Zhang, Liangxue Lai, Xiaoping Li