Modulating alternative splicing of MECP2 is a potential therapeutic strategy for Rett syndrome
调控MECP2的选择性剪接是治疗雷特综合征的一种潜在策略。
期刊:Science Translational Medicine
影响因子:14.6
doi:10.1126/scitranslmed.adq4529
Tirumala, Harini P; Wang, Li; Li, Yan; Bajikar, Sameer S; Anderson, Ashley G; Wang, Wei; Trostle, Alexander J; Zahabiyon, Mahla; Bajic, Aleksandar; Kim, Jean J; Chen, Hu; Liu, Zhandong; Zoghbi, Huda Y